AAV-delivered engineered suppressor tRNA rescues visual function in mice with an inherited retinal disease.
利用 AAV 递送的工程化抑制 tRNA 可挽救患有遗传性视网膜疾病的小鼠的视觉功能。
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-66176-y
Ren Chengda, Song Li, Hu Ming, Jin Xiu, Liang Licong, Liu Fanfei, Su Jing, Fu Jiamei, Yang Yiliu, Liu Man, Xu Qiuxia, Wu Xiaoyi, Luo Min, Ye Qin, Li Qiqi, An Yifang, Li Manjun, She Kaiqin, Wei Yuquan, Lu Fang, Yang Yang