In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of beta-thalassemia
体内筛选基因修饰的成红细胞祖细胞可实现β-地中海贫血的长期矫正。
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:9.1
doi:10.1073/pnas.0711666105
Miccio, Annarita; Cesari, Rossano; Lotti, Francesco; Rossi, Claudia; Sanvito, Francesca; Ponzoni, Maurilio; Routledge, Samantha J E; Chow, Cheok-Man; Antoniou, Michael N; Ferrari, Giuliana
