日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal Gene Therapy for Giant Axonal Neuropathy

鞘内基因疗法治疗巨轴突神经病

Bharucha-Goebel, Diana X; Todd, Joshua J; Saade, Dimah; Norato, Gina; Jain, Minal; Lehky, Tanya; Bailey, Rachel M; Chichester, Jessica A; Calcedo, Roberto; Armao, Diane; Foley, A Reghan; Mohassel, Payam; Tesfaye, Eshetu; Carlin, Bradley P; Seremula, Beth; Waite, Melissa; Zein, Wadih M; Huryn, Laryssa A; Crawford, Thomas O; Sumner, Charlotte J; Hoke, Ahmet; Heiss, John D; Charnas, Lawrence; Hooper, Jody E; Bouldin, Thomas W; Kang, Elizabeth M; Rybin, Denis; Gray, Steven J; Bönnemann, Carsten G

Limb Perfusion Delivery of a rAAV1 Alpha-1 Antitrypsin Vector in Non-Human Primates Is Safe but Insufficient for Therapy

在非人灵长类动物中,通过肢体灌注递送rAAV1 α-1抗胰蛋白酶载体是安全的,但不足以用于治疗。

Pires-Ferreira, Debora; Reil, Darcy; Tang, Qiushi; Blackwood, Meghan; Gallagher, Thomas; Keeler, Allison M; Chichester, Jessica A; Vyhnal, Kristin K; Lindborg, Jane A; Benson, Janet; Fu, Dongtao; Flotte, Terence R; Gruntman, Alisha M

Phase I study of liver depot gene therapy in late-onset Pompe disease.

针对晚发型庞贝氏症的肝脏基因治疗的I期研究

Smith Edward C, Hopkins Sam, Case Laura E, Xu Ming, Walters Crista, Dearmey Stephanie, Han Sang-Oh, Spears Tracy G, Chichester Jessica A, Bossen Edward H, Hornik Christoph P, Cohen Jennifer L, Bali Deeksha, Kishnani Priya S, Koeberl Dwight D

Erratum: Intravenous immunoglobulin prevents peripheral liver transduction of intrathecally delivered AAV vectors

更正:静脉注射免疫球蛋白可阻止鞘内注射的AAV载体在肝脏外周组织中的转导。

Horiuchi, Makoto; Hinderer, Christian J; Greig, Jenny A; Dyer, Cecilia; Buza, Elizabeth L; Bell, Peter; Chichester, Jessica A; Hayashi, Peter M; Yan, Hanying; Goode, Tamara; Wilson, James M

Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys

在幼年恒河猴中鞘内注射腺相关病毒9型后,人艾杜糖醛酸酶的表达安全且持续

Hordeaux, Juliette; Hinderer, Christian; Buza, Elizabeth L; Louboutin, Jean-Pierre; Jahan, Tahsin; Bell, Peter; Chichester, Jessica A; Tarantal, Alice F; Wilson, James M

Safety and immunogenicity of a plant-produced Pfs25 virus-like particle as a transmission blocking vaccine against malaria: A Phase 1 dose-escalation study in healthy adults

植物生产的Pfs25病毒样颗粒作为疟疾传播阻断疫苗的安全性和免疫原性:一项针对健康成年人的I期剂量递增研究

Chichester, Jessica A; Green, Brian J; Jones, R Mark; Shoji, Yoko; Miura, Kazutoyo; Long, Carole A; Lee, Cynthia K; Ockenhouse, Christian F; Morin, Merribeth J; Streatfield, Stephen J; Yusibov, Vidadi

Purification and immunogenicity of hemagglutinin from highly pathogenic avian influenza virus H5N1 expressed in Nicotiana benthamiana

在烟草中表达的高致病性禽流感病毒H5N1的血凝素的纯化和免疫原性

Pua, Teen-Lee; Chan, Xiao Ying; Loh, Hwei-San; Omar, Abdul Rahman; Yusibov, Vidadi; Musiychuk, Konstantin; Hall, Alexandra C; Coffin, Megan V; Shoji, Yoko; Chichester, Jessica A; Bi, Hong; Streatfield, Stephen J

Evaluation of inflammatory and immune responses in long-term cultured human precision-cut lung slices.

对长期培养的人类精密切割肺切片中的炎症和免疫反应进行评估

Temann Angela, Golovina Tatiana, Neuhaus Vanessa, Thompson Carolann, Chichester Jessica A, Braun Armin, Yusibov Vidadi

Immunogenicity of H1N1 influenza virus-like particles produced in Nicotiana benthamiana

本氏烟草中产生的H1N1流感病毒样颗粒的免疫原性

Shoji, Yoko; Prokhnevsky, Alex; Leffet, Brett; Vetter, Nancy; Tottey, Stephen; Satinover, Shama; Musiychuk, Konstantin; Shamloul, Moneim; Norikane, Joey; Jones, R Mark; Chichester, Jessica A; Green, Brian J; Streatfield, Stephen J; Yusibov, Vidadi

A novel plant-produced Pfs25 fusion subunit vaccine induces long-lasting transmission blocking antibody responses

一种新型植物生产的Pfs25融合亚单位疫苗可诱导持久的阻断传播抗体反应。

Jones, R Mark; Chichester, Jessica A; Manceva, Slobodanka; Gibbs, Sandra K; Musiychuk, Konstantin; Shamloul, Moneim; Norikane, Joey; Streatfield, Stephen J; van de Vegte-Bolmer, Marga; Roeffen, Will; Sauerwein, Robert W; Yusibov, Vidadi