Molecular determinants of phospholipid treatment to reduce intracellular cholesterol accumulation in NPC1 deficiency
磷脂治疗降低NPC1缺陷症中细胞内胆固醇积累的分子决定因素
期刊:Journal of Biological Chemistry
影响因子:3.9
doi:10.1016/j.jbc.2024.107889
Deng, Shikun; Liu, Ting-Ann; Ilnytska, Olga; Allada, Tamara; Fomina, Angelina; Lin, Nancy; Petukhova, Valentina Z; Pathmasiri, Koralege C; Chinthapally, Kiran; Blagg, Brian S J; Ashfeld, Brandon L; Cologna, Stephanie M; Storch, Judith