Intravitreal adenine base editing of RS1 improves vision in a preclinical mouse model of retinoschisis.
在视网膜劈裂症的临床前小鼠模型中，玻璃体内注射RS1腺嘌呤碱基编辑可改善视力。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.04.021
Jo Dong Hyun, Jang Hyewon, Cho Chang Sik, Lee Seok Jae, Heo Ji Hwa, Kim Jung Ah, Kim Se Jin, Ryu WonHyoung, Park Chan-Wook, Kang Byeong-Cheol, Gee Heon Yung, Sung Young Hoon, Kim Hyongbum Henry, Kim Jeong Hun
