日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Aberrant maintenance of developmental transcription factor PAX6 promotes neuronal cell death via JNK3 signaling.

发育转录因子 PAX6 的异常维持通过 JNK3 信号通路促进神经元细胞死亡。

Kim Ji-Young, An Mi-Jin, Kim Jinho, Kim Chul-Hong, Park Yuna, Shin Geun-Seup, Lee Hyun-Min, Jo Ah-Ra, Kim Mi Jin, Hwangbo Yujeong, Hong Tae Kyung, Kim Jee Taek, Choi Uimook, Kim Jung-Woong

Publisher Correction: The regulatory role of ACP5 in the diesel exhaust particle-induced AHR inflammatory signaling pathway in a human bronchial epithelial cell line

出版商更正:ACP5 在柴油机尾气颗粒诱导的人支气管上皮细胞系 AHR 炎症信号通路中的调控作用

Yu, Aaron; Yoon, Dankyu; An, Hye Bin; Choi, Uimook; Heo, Hye-Ryeon; Chae, Dong-Hoon; Park, Hyun Sung; Park, Jae Han; Han, Myoung Hee; Heo, Jiyoung; Cho, Keonwoo; Park, Ki-Sun; Yoo, Hee Min; Kim, Hyung-Sik; Kang, Kyung-Sun; Oh, Mi-Kyung; Lim, Hyun Joung; Yu, Kyung-Rok

The regulatory role of ACP5 in the diesel exhaust particle-induced AHR inflammatory signaling pathway in a human bronchial epithelial cell line.

ACP5 在柴油机尾气颗粒诱导的人类支气管上皮细胞系 AHR 炎症信号通路中的调控作用

Yu Aaron, Yoon Dankyu, An Hye Bin, Choi Uimook, Heo Hye-Ryeon, Chae Dong-Hoon, Park Hyun Sung, Park Jae Han, Han Myoung Hee, Heo Jiyoung, Cho Keonwoo, Park Ki-Sun, Yoo Hee Min, Kim Hyung-Sik, Kang Kyung-Sun, Oh Mi-Kyung, Lim Hyun Joung, Yu Kyung-Rok

Impact of CRISPR/HDR editing versus lentiviral transduction on long-term engraftment and clonal dynamics of HSPCs in rhesus macaques

CRISPR/HDR 编辑与慢病毒转导对恒河猴造血干细胞长期移植和克隆动态的影响

Lee, Byung-Chul; Gin, Ashley; Wu, Chuanfeng; Singh, Komudi; Grice, Max; Mortlock, Ryland; Abraham, Diana; Fan, Xing; Zhou, Yifan; AlJanahi, Aisha; Choi, Uimook; DeRavin, Suk See; Shin, Taehoon; Hong, Sogun; Dunbar, Cynthia E

High-fidelity PAMless base editing of hematopoietic stem cells to treat chronic granulomatous disease

利用高保真无PAM碱基编辑技术对造血干细胞进行治疗慢性肉芽肿病

Bzhilyanskaya, Vera; Ma, Linyuan; Liu, Siyuan; Fox, Lauren R; Whittaker, Madelynn N; Meis, Ronald J; Choi, Uimook; Lawson, Amanda; Ma, Michelle; Theobald, Narda; Burkett, Sandra; Sweeney, Colin L; Lazzarotto, Cicera R; Tsai, Shengdar Q; Lack, Justin B; Wu, Xiaolin; Dahl, Gary A; Malech, Harry L; Kleinstiver, Benjamin P; De Ravin, Suk See

CRISPR/Cas9-mediated Cxcr4 disease allele inactivation for gene therapy in a mouse model of WHIM syndrome

利用 CRISPR/Cas9 介导的 Cxcr4 致病等位基因失活技术在 WHIM 综合征小鼠模型中进行基因治疗

Gao, Ji-Liang; Owusu-Ansah, Albert; Yang, Alexander; Yim, Erin; McDermott, David H; Jacobs, Paejonette; Majumdar, Shamik; Choi, Uimook; Sweeney, Colin L; Malech, Harry L; Murphy, Philip M

Enhanced homology-directed repair for highly efficient gene editing in hematopoietic stem/progenitor cells

增强同源定向修复以实现造血干/祖细胞中高效的基因编辑

De Ravin, Suk See; Brault, Julie; Meis, Ronald J; Liu, Siyuan; Li, Linhong; Pavel-Dinu, Mara; Lazzarotto, Cicera R; Liu, Taylor; Koontz, Sherry M; Choi, Uimook; Sweeney, Colin L; Theobald, Narda; Lee, GaHyun; Clark, Aaron B; Burkett, Sandra S; Kleinstiver, Benjamin P; Porteus, Matthew H; Tsai, Shengdar; Kuhns, Douglas B; Dahl, Gary A; Headey, Stephen; Wu, Xiaolin; Malech, Harry L

AB021. Histopathologic characteristics of resected thymic cyst walls, with imaging correlation

AB021. 切除的胸腺囊肿壁的组织病理学特征及其与影像学的相关性

Brault, Julie; Liu, Taylor; Bello, Ezekiel; Liu, Siyuan; Sweeney, Colin L; Meis, Ronald J; Koontz, Sherry; Corsino, Cristina; Choi, Uimook; Vayssiere, Guillaume; Bosticardo, Marita; Dowdell, Kennichi; Lazzarotto, Cicera R; Clark, Aaron B; Notarangelo, Luigi D; Ravell, Juan C; Lenardo, Michael J; Kleinstiver, Benjamin P; Tsai, Shengdar Q; Wu, Xiaolin; Dahl, Gary A; Malech, Harry L; De Ravin, Suk See; Villalba, Julian A; Louissaint, Abner Jr; Haramati, Adina; Ackman, Jeanne B

Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47(phox)-Deficient Chronic Granulomatous Disease

针对p47(phox)缺陷型慢性肉芽肿病的新型慢病毒基因疗法的临床前优化和安全性研究

Schejtman, Andrea; Vetharoy, Winston; Choi, Uimook; Rivat, Christine; Theobald, Narda; Piras, Giuseppa; Leon-Rico, Diego; Buckland, Karen; Armenteros-Monterroso, Elena; Benedetti, Sara; Ashworth, Michael T; Rothe, Michael; Schambach, Axel; Gaspar, Hubert Bobby; Kang, Elizabeth M; Malech, Harry L; Thrasher, Adrian J; Santilli, Giorgia

Lentiviral gene therapy for X-linked chronic granulomatous disease

慢病毒基因疗法治疗X连锁慢性肉芽肿病

Kohn, Donald B; Booth, Claire; Kang, Elizabeth M; Pai, Sung-Yun; Shaw, Kit L; Santilli, Giorgia; Armant, Myriam; Buckland, Karen F; Choi, Uimook; De Ravin, Suk See; Dorsey, Morna J; Kuo, Caroline Y; Leon-Rico, Diego; Rivat, Christine; Izotova, Natalia; Gilmour, Kimberly; Snell, Katie; Dip, Jinhua Xu-Bayford; Darwish, Jinan; Morris, Emma C; Terrazas, Dayna; Wang, Leo D; Bauser, Christopher A; Paprotka, Tobias; Kuhns, Douglas B; Gregg, John; Raymond, Hayley E; Everett, John K; Honnet, Geraldine; Biasco, Luca; Newburger, Peter E; Bushman, Frederic D; Grez, Manuel; Gaspar, H Bobby; Williams, David A; Malech, Harry L; Galy, Anne; Thrasher, Adrian J