Treating Transthyretin Amyloidosis via Adeno-Associated Virus Vector Delivery of Meganucleases
利用腺相关病毒载体递送巨核酸酶治疗转甲状腺素蛋白淀粉样变性
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2022.061
Greig, Jenny A; Breton, Camilo; Ashley, Scott N; Martins, Kelly M; Gorsuch, Cassandra; Chorazeczewski, Joanna K; Furmanak, Thomas; Smith, Melanie K; Zhu, Yanqing; Bell, Peter; Shoop, Wendy; Li, Hui; Smith, Jeff; Tomberlin, Ginger; Clark, Peter; Mitchell, Thomas W; Buza, Elizabeth L; Yan, Hanying; Jantz, Derek; Wilson, James M