Longitudinal changes in clinical outcome measures in COL6-related dystrophies and LAMA2-related dystrophies
COL6相关肌营养不良症和LAMA2相关肌营养不良症临床结果指标的纵向变化
期刊:Neurology
影响因子:8.5
doi:10.1212/WNL.0000000000008517
Jain, Minal S; Meilleur, Katherine; Kim, Eunhee; Norato, Gina; Waite, Melissa; Nelson, Leslie; McGuire, Michelle; Duong, Tina; Keller, Katherine; Lott, Donovan J; Glanzman, Allan; Rose, Kristy; Main, Marion; Fiorini, Courtney; Chrismer, Irene; Linton, Melody; Punjabi, Monal; Elliott, Jeffrey; Tounkara, Fatoumata; Vasavada, Ruhi; Logaraj, Ranjani; Winkert, Jocelyn; Donkervoort, Sandra; Leach, Meganne; Dastgir, Jahannaz; Hynan, Linda; Nichols, Carmel; Hartnett, Elizabeth; Averion, Gilberto M; Collins, James C; Kim, Eunice S; Kokkinis, Angela; Schindler, Alice; Zukosky, Kristen; Fee, Robert; Hinton, Veronica; Mohassel, Payam; Bharucha-Goebel, Diana; Vuillerot, Carole; McGraw, Peter; Barton, Mark; Fontana, Joseph; Rutkowski, Anne; Foley, A Reghan; Bönnemann, Carsten G