日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Diagnostic Test Characteristics of Ultrasound-Based Hydronephrosis for Chronic Kidney Disease in Children and Adolescents With Myelomeningocele: Results From the UMPIRE and National Spina Bifida Patient Registry Cohort Studies

超声检查在脊髓脊膜膨出患儿及青少年慢性肾脏病诊断中肾积水的诊断试验特征:来自 UMPIRE 和国家脊柱裂患者登记队列研究的结果

Chu, David I; Liu, Tiebin; Williams, Tonya; Mix, Jacqueline; Ahn, Jennifer; Austin, J Christopher; Baum, Michelle; Clayton, Douglass; Jarosz, Susan; Joseph, David; Roth, Elizabeth; Routh, Jonathan; Tu, Duong; Vasquez, Evalynn; Wallis, M Chad; Wiener, John; Cheng, Earl; Yerkes, Elizabeth; Tanaka, Stacy

Design and Methodological Considerations of the Centers for Disease Control and Prevention Urologic and Renal Protocol for the Newborn and Young Child with Spina Bifida

美国疾病控制与预防中心针对患有脊柱裂的新生儿和幼儿的泌尿系统和肾脏诊疗方案的设计和方法学考虑

Routh, Jonathan C; Cheng, Earl Y; Austin, J Christopher; Baum, Michelle A; Gargollo, Patricio C; Grady, Richard W; Herron, Adrienne R; Kim, Steven S; King, Shelly J; Koh, Chester J; Paramsothy, Pangaja; Raman, Lisa; Schechter, Michael S; Smith, Kathryn A; Tanaka, Stacy T; Thibadeau, Judy K; Walker, William O; Wallis, M Chad; Wiener, John S; Joseph, David B

Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency

穿孔素基因转移到造血干细胞可改善穿孔素缺乏小鼠模型中的免疫失调

Marlene Carmo, Kimberly A Risma, Paritha Arumugam, Swati Tiwari, Adrianne E Hontz, Claudia A Montiel-Equihua, Maria E Alonso-Ferrero, Michael P Blundell, Axel Schambach, Christopher Baum, Punam Malik, Adrian J Thrasher, Michael B Jordan, H Bobby Gaspar

Non-integrating gamma-retroviral vectors as a versatile tool for transient zinc-finger nuclease delivery

非整合型γ逆转录病毒载体作为瞬时锌指核酸酶递送的多功能工具

Sylwia Bobis-Wozowicz, Melanie Galla, Jamal Alzubi, Johannes Kuehle, Christopher Baum, Axel Schambach, Toni Cathomen

Preclinical safety and efficacy of an anti-HIV-1 lentiviral vector containing a short hairpin RNA to CCR5 and the C46 fusion inhibitor

含有 CCR5 短发夹 RNA 和 C46 融合抑制剂的抗 HIV-1 慢病毒载体的临床前安全性和有效性

Orit Wolstein, Maureen Boyd, Michelle Millington, Helen Impey, Joshua Boyer, Annett Howe, Frederic Delebecque, Kenneth Cornetta, Michael Rothe, Christopher Baum, Tamara Nicolson, Rachel Koldej, Jane Zhang, Naomi Keech, Joanna Camba Colón, Louis Breton, Jeffrey Bartlett, Dong Sung An, Irvin Sy Chen, 

Sleeping Beauty transposon-based system for cellular reprogramming and targeted gene insertion in induced pluripotent stem cells

基于睡美人转座子的诱导多能干细胞细胞重编程和靶向基因插入系统

Ivana Grabundzija, Jichang Wang, Attila Sebe, Zsuzsanna Erdei, Robert Kajdi, Anantharam Devaraj, Doris Steinemann, Károly Szuhai, Ulrike Stein, Tobias Cantz, Axel Schambach, Christopher Baum, Zsuzsanna Izsvák, Balázs Sarkadi, Zoltán Ivics

Alpharetroviral vector-mediated gene therapy for X-CGD: functional correction and lack of aberrant splicing

α逆转录病毒载体介导的X-CGD基因治疗:功能矫正和异常剪接的缺失

Kerstin B Kaufmann, Christian Brendel, Julia D Suerth, Uta Mueller-Kuller, Linping Chen-Wichmann, Joachim Schwäble, Shweta Pahujani, Hana Kunkel, Axel Schambach, Christopher Baum, Manuel Grez

Highly significant antiviral activity of HIV-1 LTR-specific tre-recombinase in humanized mice

HIV-1 LTR 特异性 tre 重组酶在人源化小鼠中具有高度显著的抗病毒活性

Ilona Hauber, Helga Hofmann-Sieber, Jan Chemnitz, Danilo Dubrau, Janet Chusainow, Rolf Stucka, Philip Hartjen, Axel Schambach, Patrick Ziegler, Karl Hackmann, Evelin Schröck, Udo Schumacher, Christoph Lindner, Adam Grundhoff, Christopher Baum, Markus G Manz, Frank Buchholz, Joachim Hauber

Pharmacological targeting of the thrombomodulin-activated protein C pathway mitigates radiation toxicity

血栓调节蛋白活化蛋白 C 通路的药理学靶向作用可减轻放射毒性

Hartmut Geiger, Snehalata A Pawar, Edward J Kerschen, Kalpana J Nattamai, Irene Hernandez, Hai Po H Liang, Jose Á Fernández, Jose A Cancelas, Marnie A Ryan, Olga Kustikova, Axel Schambach, Qiang Fu, Junru Wang, Louis M Fink, Karl-Uwe Petersen, Daohong Zhou, John H Griffin, Christopher Baum, Hartmut

Alpharetroviral self-inactivating vectors: long-term transgene expression in murine hematopoietic cells and low genotoxicity

α逆转录病毒自灭活载体:在小鼠造血细胞中长期转基因表达且遗传毒性低

Julia D Suerth, Tobias Maetzig, Martijn H Brugman, Niels Heinz, Jens-Uwe Appelt, Kerstin B Kaufmann, Manfred Schmidt, Manuel Grez, Ute Modlich, Christopher Baum, Axel Schambach