Engineered mischarged transfer RNAs for correcting pathogenic missense mutations
工程化错排转移 RNA 用于纠正致病错义突变
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2023.12.014
Yichen Hou, Wen Zhang, Philip T McGilvray, Marek Sobczyk, Tianxin Wang, Shao Huan Samuel Weng, Allen Huff, Sihao Huang, Noah Pena, Christopher D Katanski, Tao Pan