日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Precision and efficacy of RNA-guided DNA integration in high-expressing muscle loci

RNA 引导 DNA 整合在高表达肌肉基因座中的精确度和有效性

Made Harumi Padmaswari, Gabrielle Bulliard, Shilpi Agrawal, Mary S Jia, Sabin Khadgi, Kevin A Murach, Christopher E Nelson

Optimizing Recombinant Cas9 Expression: Insights from E. coli BL21(DE3) Strains for Enhanced Protein Purification and Genome Editing

优化重组 Cas9 表达:从大肠杆菌 BL21(DE3) 菌株中获取增强蛋白质纯化和基因组编辑的见解

Shilpi Agrawal, Made Harumi Padmaswari, Abbey L Stokes, Daniel Maxenberger, Morgan Reese, Adila Khalil, Christopher E Nelson

Longitudinal examination of perfusion and angiogenesis markers in primary colorectal tumors shows distinct signatures for metronomic and maximum-tolerated dose strategies

对原发性结直肠肿瘤灌注和血管生成标志物的纵向检查显示,节拍剂量和最大耐受剂量策略具有不同的特征

Ariel I Mundo, Abdussaboor Muhammad, Kerlin Balza, Christopher E Nelson, Timothy J Muldoon

Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine models

Cas9 特异性免疫反应影响多种营养不良犬模型中的局部和全身 AAV CRISPR 疗法

Chady H Hakim, Sandeep R P Kumar #, Dennis O Pérez-López #, Nalinda B Wasala, Dong Zhang, Yongping Yue, James Teixeira, Xiufang Pan, Keqing Zhang, Emily D Million, Christopher E Nelson, Samantha Metzger, Jin Han, Jacqueline A Louderman, Florian Schmidt, Feng Feng, Dirk Grimm, Bruce F Smith, Gang Yao

Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystrophy

AAV-CRISPR 基因组编辑对杜氏肌营养不良症的长期评估

Christopher E Nelson, Yaoying Wu, Matthew P Gemberling, Matthew L Oliver, Matthew A Waller, Joel D Bohning, Jacqueline N Robinson-Hamm, Karen Bulaklak, Ruth M Castellanos Rivera, Joel H Collier, Aravind Asokan, Charles A Gersbach

Targeted transcriptional modulation with type I CRISPR-Cas systems in human cells

使用 I 型 CRISPR-Cas 系统在人类细胞中进行靶向转录调控

Adrian Pickar-Oliver, Joshua B Black, Mae M Lewis, Kevin J Mutchnick, Tyler S Klann, Kylie A Gilcrest, Madeleine J Sitton, Christopher E Nelson, Alejandro Barrera, Luke C Bartelt, Timothy E Reddy, Chase L Beisel, Rodolphe Barrangou, Charles A Gersbach

RNA-guided transcriptional silencing in vivo with S. aureus CRISPR-Cas9 repressors

利用金黄色葡萄球菌 CRISPR-Cas9 抑制剂进行 RNA 引导的体内转录沉默

Pratiksha I Thakore, Jennifer B Kwon, Christopher E Nelson, Douglas C Rouse, Matthew P Gemberling, Matthew L Oliver, Charles A Gersbach

AAV CRISPR editing rescues cardiac and muscle function for 18 months in dystrophic mice

AAV CRISPR 编辑挽救了营养不良小鼠 18 个月的心脏和肌肉功能

Chady H Hakim, Nalinda B Wasala, Christopher E Nelson, Lakmini P Wasala, Yongping Yue, Jacqueline A Louderman, Thais B Lessa, Aihua Dai, Keqing Zhang, Gregory J Jenkins, Michael E Nance, Xiufang Pan, Kasun Kodippili, N Nora Yang, Shi-Jie Chen, Charles A Gersbach, Dongsheng Duan

Generation and comparison of CRISPR-Cas9 and Cre-mediated genetically engineered mouse models of sarcoma

CRISPR-Cas9 和 Cre 介导的肉瘤基因工程小鼠模型的建立及比较

Jianguo Huang, Mark Chen, Melodi Javid Whitley, Hsuan-Cheng Kuo, Eric S Xu, Andrea Walens, Yvonne M Mowery, David Van Mater, William C Eward, Diana M Cardona, Lixia Luo, Yan Ma, Omar M Lopez, Christopher E Nelson, Jacqueline N Robinson-Hamm, Anupama Reddy, Sandeep S Dave, Charles A Gersbach, Rebecca

Oligoproline-derived nanocarrier for dual stimuli-responsive gene delivery

用于双刺激响应基因传递的寡脯氨酸衍生纳米载体

Mukesh K Gupta, Sue Hyun Lee, Spencer W Crowder, Xintong Wang, Lucas H Hofmeister, Christopher E Nelson, Leon M Bellan, Craig L Duvall, Hak-Joon Sung