Combining nonsense mutation suppression therapy with nonsense-mediated decay inhibition in neurofibromatosis type 1
将无义突变抑制疗法与无义介导衰变抑制疗法相结合治疗 1 型神经纤维瘤病
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2023.06.018
Sara H Osum, Eunice I Oribamise, Stanislas M A S Corbière, Mandy Taisto, Tyler Jubenville, Alex Coutts, Mark N Kirstein, James Fisher, Christopher Moertel, Ming Du, David Bedwell, David A Largaespada, Adrienne L Watson
