Genetically corrected RAG2-SCID human hematopoietic stem cells restore V(D)J-recombinase and rescue lymphoid deficiency
基因校正的RAG2-SCID人类造血干细胞可恢复V(D)J重组酶并挽救淋巴细胞缺陷
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2023011766
Pavel-Dinu, Mara; Gardner, Cameron L; Nakauchi, Yusuke; Kawai, Tomoki; Delmonte, Ottavia M; Palterer, Boaz; Bosticardo, Marita; Pala, Francesca; Viel, Sebastien; Malech, Harry L; Ghanim, Hana Y; Bode, Nicole M; Kurgan, Gavin L; Detweiler, Angela M; Vakulskas, Christopher A; Neff, Norma F; Sheikali, Adam; Menezes, Sherah T; Chrobok, Jade; Hernández González, Elaine M; Majeti, Ravindra; Notarangelo, Luigi D; Porteus, Matthew H