Safety and efficacy of a fitusiran antithrombin-based dose regimen in people with hemophilia A or B: the ATLAS-OLE study
在A型或B型血友病患者中,基于fitusiran抗凝血酶的给药方案的安全性和有效性:ATLAS-OLE研究
期刊:Blood
影响因子:23.1
doi:10.1182/blood.2024027008
Young, Guy; Kavakli, Kaan; Klamroth, Robert; Matsushita, Tadashi; Peyvandi, Flora; Pipe, Steven W; Rangarajan, Savita; Shen, Ming-Ching; Srivastava, Alok; Sun, Jing; Tran, Huyen; You, Chur-Woo; Zülfikar, Bülent; Menapace, Laurel A; Zhang, Chuanwu; Shen, Yuqian; Puurunen, Marja; Demissie, Marek; Kenet, Gili