日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Longitudinal Changes of Fundus Autofluorescence and Correlation With Visual Acuity in ABCA4-Associated Stargardt Disease

ABCA4相关Stargardt病患者眼底自发荧光纵向变化及其与视力的相关性

Ibukun, Folahan; Strauss, Rupert W; Rustam, Zainab; Khan, Muhammad Jehanzeb; Cideciyan, Artur V; Birch, David G; Ho, Alexander; Sunness, Janet S; Audo, Isabelle S; Michaelides, Michel; Zrenner, Eberhart; Traboulsi, Elias I; Bernstein, Paul; Sadda, SriniVas; Ip, Michael S; West, Sheila; Kong, Xiangrong

Gene therapy for young children with congenital blindness

基因疗法用于治疗先天性失明的幼儿

Cideciyan, Artur V; Aleman, Tomas S

Recovery of cone-mediated vision in Lebercilin associated retinal ciliopathy after gene therapy: One-year results of a phase I/II trial

基因治疗后,莱伯西林相关性视网膜纤毛病患者视锥细胞介导的视觉功能恢复:一项 I/II 期试验的一年结果

Aleman, Tomas S; Uyhazi, Katherine E; Roman, Alejandro J; Weber, Mariejel L; O'Neil, Erin C; Swider, Malgorzata; Sumaroka, Alexander; Maguire, Katherine H; Aleman, Elena M; Santos, Arlene J; Kim, Rebecca J; Parchinski, Kelsey M; Billek, Andrew; Fradin, Makayla; Chung, William; Margaritis, Paris; Sun, Junwei; Scoles, Drew H; Wu, Vivian; Garafalo, Alexandra V; Jayagopal, Ashwath; Yerxa, Ben; Tuller, Sarah; Maguire, Albert M; Bennett, Jean; Cideciyan, Artur V

Measuring Rod- and Cone-Photoreceptor-Specific Vision in Inherited Retinal Diseases Using a Commercial Perimeter

使用商用视野计测量遗传性视网膜疾病患者的视杆细胞和视锥细胞特异性视力

Wu, Vivian; Roman, Alejandro J; Galsterer, Emma L; Ansari, Georg; Erdinest, Inbar; Righetti, Giulia; Viarbitskaya, Iryna; Russell, Robert C; Kim, Rebecca J; Charlier, Jacques; Pfau, Kristina; Stingl, Krunoslav; Banin, Eyal; Pfau, Maximilian; Stingl, Katarina; Aleman, Tomas S; Cideciyan, Artur V

Location and Identity of Photoreceptors Contributing to the Full-Field Stimulus Test (FST)

参与全视野刺激测试 (FST) 的光感受器的位置和类型

Cideciyan, Artur V; Neuhauser, Hongsong; Roman, Alejandro J; Aleman, Tomas S

Photoreceptor Disease at Ambiguous Transition Zones in Inherited Retinal Degenerations

遗传性视网膜变性中模糊过渡区的感光细胞疾病

Sumaroka, Alexander; Swider, Malgorzata; Aleman, Tomas S; Cideciyan, Artur V

Addressing Challenges in Developing Treatments for Inherited Retinal Diseases: Recommendations From the Third Monaciano Symposium

应对遗传性视网膜疾病治疗研发中的挑战:第三届莫纳恰诺研讨会的建议

Thompson, Debra A; Jayasundera, K Thiran; Alekseev, Oleg; Ali, Robin R; Amato, Alessia; Arshavsky, Vadim Y; Audo, Isabelle S; Auricchio, Alberto; Bainbridge, James W B; Banin, Eyal; Besirli, Cagri G; Birch, David G; Branham, Kari E; Cideciyan, Artur V; Daiger, Stephen P; Duncan, Jacque L; Fahim, Abigail T; Flannery, John G; Gattegna, Roberto; Heckenlively, John R; Héon, Elise; Iannaccone, Alessandro; Khan, Naheed W; Khateb, Samer; Klassen, Henry J; Leroy, Bart P; Marangoni, Dario; Michaelides, Michel; Musch, David C; Pennesi, Mark E; Petersen-Jones, Simon M; Pierce, Eric A; Rao, Rajesh C; Sahel, José-Alain; Sieving, Paul A; Strettoi, Enrica; Strong, Cameron R; Wubben, Thomas J; Yang, Paul; Zacks, David N

Retinal prolactin isoform PRLΔE1 sustains rod disease in inherited retinal degenerations

视网膜催乳素同工型PRLΔE1在遗传性视网膜变性中维持视杆细胞疾病

Raghavi Sudharsan,Jennifer Kwok,Malgorzata Swider,Alexander Sumaroka,Gustavo D Aguirre,Artur V Cideciyan,William A Beltran

Evaluation of Retinal Structure and Visual Function in Blue Cone Monochromacy to Develop Clinical Endpoints for L-opsin Gene Therapy

评估蓝锥单色视患者的视网膜结构和视觉功能,以建立L-视蛋白基因治疗的临床终点

Cideciyan, Artur V; Roman, Alejandro J; Warner, Raymond L; Sumaroka, Alexander; Wu, Vivian; Jiang, Yu Y; Swider, Malgorzata; Garafalo, Alexandra V; Viarbitskaya, Iryna; Russell, Robert C; Kohl, Susanne; Wissinger, Bernd; Ripamonti, Caterina; Barbur, John L; Bach, Michael; Carroll, Joseph; Morgan, Jessica I W; Aleman, Tomas S

Nogo-A is secreted in extracellular vesicles, occurs in blood and can influence vascular permeability

Nogo-A由细胞外囊泡分泌,存在于血液中,并可影响血管通透性。

Ruslan Rust ,Mea M Holm ,Matteo Egger ,Oliver Weinmann ,Daniёlle van Rossum ,Fruzsina R Walter ,Ana Raquel Santa-Maria ,Lisa Grönnert ,Michael A Maurer ,Simon Kraler ,Alexander Akhmedov ,Rose Cideciyan ,Thomas F Lüscher ,Maria A Deli ,Inge K Herrmann ,Martin E Schwab