Striated muscle-specific base editing enables correction of mutations causing dilated cardiomyopathy
横纹肌特异性碱基编辑能够纠正引起扩张型心肌病的突变
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-023-39352-1
Markus Grosch, Laura Schraft, Adrian Chan, Leonie Küchenhoff, Kleopatra Rapti, Anne-Maud Ferreira, Julia Kornienko, Shengdi Li, Michael H Radke, Chiara Krämer, Sandra Clauder-Münster, Emerald Perlas, Johannes Backs, Michael Gotthardt, Christoph Dieterich, Maarten M G van den Hoogenhof, Dirk Grimm, L