日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Health care resources and costs associated with delivering gene therapy for hemophilia in clinical practice

在临床实践中,为血友病患者提供基因治疗所涉及的医疗资源和成本

Prameyllawati, Diaz M; Mussert, Caroline M A; Oude Voshaar, Martijn A H; Lingsma, Hester F; Cnossen, Marjon H; Coppens, Michiel; Meijer, Karina; van der Valk, Paul R; Leebeek, Frank W G; Ten Ham, Renske M T

A Systematic Review of Modelling Approaches in Economic Evaluations of Treatments for Inherited Bleeding Disorders

遗传性出血性疾病治疗经济评价中建模方法的系统性综述

Prameyllawati, Diaz M; Lingsma, Hester F; Cnossen, Marjon H; Ten Ham, Renske M T

In Silico Assessment of Limited Blood Sampling Strategies for Individualised Pharmacokinetic-guided Dosing of Efanesoctocog Alfa in Haemophilia A Patients

利用计算机模拟评估有限血液采样策略在A型血友病患者个体化药代动力学指导的依非尼奥托克α给药中的应用

den Hollander, Jelien; Cnossen, Marjon H; Mathôt, Ron A A

Clinical Frailty Scale, Surprise Question and 1-year Mortality in Older Patients with Advanced CKD

临床衰弱量表、意外问题与晚期慢性肾脏病老年患者1年死亡率

Demirhan, Imre; Jongejan, Micha; van Oevelen, Mathijs; Kiriwenno, Keanu; Mooijaart, Simon P; Verhaar, Marianne C; Bos, Willem Jan W; Joosten, Hanneke; Cnossen, Trijntje T; van Buren, Marjolijn; Abrahams, Alferso C

Outcomes after (chemo)radiotherapy for anal cancer - A nationwide cohort study

肛门癌(化疗)放疗后的疗效——一项全国性队列研究

Deijen, C L; Berbée, M; Geijsen, E D; Neelis, K J; Wee, L; Bakker-Van der Jagt, M A B; Boer, A H; Ceha, H M; Cnossen, J S; Intven, M P W; Leseman-Hoogenboom, M M; Mulder-Ebrahimi, G; Muller, K; Oppedijk, V; Reerink, O; Rütten, H; Spruit, P H; van Triest, B

Clinical phenotype and pathophysiological mechanisms underlying qualitative low VWF

临床表型和低VWF相关的病理生理机制

Atiq, Ferdows; Blok, Robin; van Kwawegen, Calvin B; Hulshof, Anne-Marije; Doherty, Dearbhla; Lavin, Michelle; van der Bom, Johanna G; O'Connell, Niamh M; de Meris, Joke; Ryan, Kevin; Schols, Saskia E M; van Heerde, Waander L; Doyle, Mairead; Byrne, Mary; Heubel-Moenen, Floor C J I; van Galen, Karin P M; Preston, Roger J S; Cnossen, Marjon H; Fijnvandraat, Karin; Baker, Ross I; Meijer, Karina; James, Paula; Di Paola, Jorge; Eikenboom, Jeroen; Leebeek, Frank W G; O'Donnell, James S

Replacement therapy in pregnant women with von Willebrand disease during delivery: Factor levels and pharmacokinetics

妊娠期血管性血友病患者分娩期间的替代疗法:因子水平和药代动力学

Al Arashi, Wala; Cloesmeijer, Michael E; Leebeek, Frank W G; Duvekot, Johannes J; Kruip, Marieke J H A; Mathôt, Ron A A; Cnossen, Marjon H

Pyruvate Kinase Function Correlates With Red Blood Cell Properties and Clinical Manifestations in Sickle Cell Disease

丙酮酸激酶功能与镰状细胞病的红细胞特性和临床表现相关

Traets, M J M; Bos, J F; van der Veen, S; van Pelt, L; van Dijk, M J; van Oirschot, B A; de Wilde, J R A; Jans, J J; van Solinge, W W; Schols, S E M; Lauw, M N; Cnossen, M H; Nur, E; Biemond, B J; Rijneveld, A W; van Beers, E J; van Wijk, R; Rab, M A E

Iron Deficiency in HbSC Disease Treated With Repetitive Phlebotomy Is Associated With Fewer Sickle Cell Disease-Related Complications

反复放血治疗HbSC病患者的缺铁性贫血与镰状细胞病相关并发症减少有关

Traets, Marissa J M; Kidane Gembremeskel, Aida S; Eijkelenboom-Bos, Jennifer; van Oirschot, Birgitte A; van der Veen, Sigrid; Russcher, Henk; van Solinge, Wouter W; Lauw, Mandy N; Nur, Erfan; Biemond, Bart J; Cnossen, Marjon H; Rijneveld, Anita W; van Wijk, Richard; van Beers, Eduard J; Rab, Minke A E

Development of an intranasal, universal influenza vaccine in an EU-funded public-private partnership: the FLUniversal consortium

欧盟资助的公私合作项目——FLUniversal联盟——正在开发一种鼻内通用流感疫苗。

Cnossen, Victor M; Moreira, Paula C Leao; Engelhardt, Othmar G; Samolej, Jerzy; Groeneveld, Geert H; Jochems, Simon P; Huisman, Wesley; Pedersen, Gabriel K; Wørzner, Katharina; Recek, Lukas; Piccini, Giulia; Trombetta, Claudia M; Aspelund, Amy; Hoag, Alaura; Reiter, Manfred; Wick, Carrie; Muster, Thomas; Kamerling, Ingrid Maria Catharina