日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

CNM-Au8 在肌萎缩侧索硬化症中的应用:HEALEY ALS 平台试验

Berry, James D; Maragakis, Nicholas J; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Stommel, Elijah W; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin J; Simmons, Zachary; Miller, Timothy; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo Jr; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney E; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Rynders, Austin; Evan, Jacob; Evan, Jeremy; Hartford, Alan; Sepassi, Marjan; Ho, Karen S; Glanzman, Robert; Greenberg, Benjamin; Hotchkin, Michael T; Paganoni, Sabrina; Cudkowicz, Merit E

Pridopidine in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial

普利多吡啶治疗肌萎缩侧索硬化症:HEALEY ALS平台试验

Shefner, Jeremy M; Oskarsson, Björn; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Heiman-Patterson, Terry; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; D'Agostino, Derek; Tustison, Eric; Scirocco, Erica; Giacomelli, Elisa; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Ajroud-Driss, Senda; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard A; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Leitner, Melanie L; Chen, Kelly; Goldberg, Y Paul; Cohen, Yael; Geva, Michal; Hayden, Michael R; Paganoni, Sabrina; Cudkowicz, Merit E

Verdiperstat in Amyotrophic Lateral Sclerosis: Results From the Randomized HEALEY ALS Platform Trial

Verdiperstat治疗肌萎缩侧索硬化症:来自随机HEALEY ALS平台试验的结果

Andrews, Jinsy; Paganoni, Sabrina; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joseph; McGlothlin, Anna; Young, Eufrosina; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney; Yu, Hong; Sherman, Alex; Shefner, Jeremy; Hall, Meghan; Kittle, Gale; Connolly, Mariah R; Berry, James D; D'Agostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Heitzman, Daragh; Ajroud-Driss, Senda; Appel, Stanley H; Shroff, Sheetal; Katz, Jonathan; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Goutman, Stephen A; Olney, Nicholas; Miller, Timothy; Fernandes, Joseph Americo; Ilieva, Hristelina; Jawdat, Omar; Weiss, Michael D; Foster, Laura; Vu, Tuan; Ladha, Shafeeq; Owegi, Margaret Ayo; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Swenson, Andrea; Heiman-Patterson, Terry; Caress, James; Fee, Dominic; Peltier, Amanda; Lewis, Richard; Rosenfeld, Jeffrey; Walk, David; Johnson, Kristin; Elliott, Matthew; Kasarskis, Edward J; Rutkove, Seward; McIlduff, Courtney E; Bedlack, Richard; Elman, Lauren; Goyal, Namita A; Rezania, Kourosh; Twydell, Paul; Benatar, Michael; Glass, Jonathan; Cohen, Jeffrey A; Jones, Vovanti; Zilliox, Lindsay; Wymer, James P; Beydoun, Said R; Shah, Jaimin; Pattee, Gary L; Martinez-Thompson, Jennifer; Nayar, Shakti; Granit, Volkan; Donohue, Mary; Grossman, Katheryn; Campbell, Daniel J; Qureshi, Irfan A; Cudkowicz, Merit E; Babu, Suma

Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial

Zilucoplan治疗肌萎缩侧索硬化症的疗效和安全性:一项随机临床试验

Paganoni, Sabrina; Fournier, Christina N; Macklin, Eric A; Chibnik, Lori B; Quintana, Melanie; Saville, Benjamin R; Detry, Michelle A; Vestrucci, Matteo; Marion, Joe; McGlothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A; Yu, Hong; Sherman, Alexander V; Shefner, Jeremy M; Hall, Meghan; Kittle, Gale; Berry, James D; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J; Simmons, Zachary; Miller, Timothy M; Olney, Nicholas; Weiss, Michael D; Goutman, Stephen A; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S; Arcila-Londono, Ximena; Jackson, Carlayne E; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Bedlack, Richard; Kasarskis, Edward J; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; McIlduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A; Cohen, Jeffrey A; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R; Wymer, James P; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W; Cudkowicz, Merit E

Volumetric MRI Comparing Longitudinal Change in MOGAD to NMOSD, MS and Healthy Controls, and Disability Associations

利用体积磁共振成像比较 MOGAD 与 NMOSD、MS 和健康对照组的纵向变化以及残疾关联

Kunchok, Amy; Amin, Moein; Ongphichetmetha, Tatchaporn; Du, Mengke; Bermel, Robert; Harvey, Tucker; Abbatemarco, Justin R; Jones, Stephen E; Cohen, Jeffrey A; Ontaneda, Daniel; Nakamura, Kunio

Progressive Myelitis in a 63-Year-Old Woman: A Case Report From the National Multiple Sclerosis Society Case Conference Proceedings

一名63岁女性的进行性脊髓炎:来自美国国家多发性硬化症协会病例研讨会的病例报告

DiMauro, Kimberly A; Heber, Morgan E; Lee, Jonathan; Cohen, Jeffrey A; Flanagan, Eoin P; Riley, Claire; Goldman, Myla D; Zamvil, Scott S; Kunchok, Amy C

Prospective SARS-CoV-2 additional vaccination in immunosuppressant-treated individuals with autoimmune diseases in a randomized controlled trial

在一项随机对照试验中,对接受免疫抑制剂治疗的自身免疫性疾病患者进行SARS-CoV-2额外疫苗接种的预期效果

Mackay, Meggan; Wagner, Catriona A; Pinckney, Ashley; Cohen, Jeffrey A; Wallace, Zachary S; Khosroshahi, Arezou; Sparks, Jeffrey A; Lord, Sandra; Saxena, Amit; Caricchio, Roberto; Kim, Alfred Hj; Kamen, Diane L; Koumpouras, Fotios; Askanase, Anca D; Smith, Kenneth; Guthridge, Joel M; Pardo, Gabriel; Mao-Draayer, Yang; Macwana, Susan; McCarthy, Sean; Sherman, Matthew A; Daneshfar Hamrah, Sanaz; Veri, Maria; Walker, Sarah; York, Kate; Tedeschi, Sara K; Wang, Jennifer; Dziubla, Gabrielle E; Castro, Mike; Carroll, Robin; Narpala, Sandeep R; Lin, Bob C; Serebryannyy, Leonid; McDermott, Adrian B; Barry, William T; Goldmuntz, Ellen; McNamara, James; Payne, Aimee S; Bar-Or, Amit; Khanna, Dinesh; James, Judith A

Brain atrophy and associations with long-term disability and cognitive function in participants with relapsing multiple sclerosis treated with ozanimod: Results from phase 3 and open-label extension trials

奥扎尼莫德治疗复发型多发性硬化症患者的脑萎缩及其与长期残疾和认知功能的关系:来自 3 期和开放标签扩展试验的结果

Cohen, Jeffrey A; Arnold, Douglas L; DeLuca, John; Hartung, Hans-Peter; Kappos, Ludwig; Comi, Giancarlo; Selmaj, Krzysztof; Steinman, Lawrence; Bar-Or, Amit; Montalban, Xavier; Havrdová, Eva K; Sheffield, James K; Pachai, Chahin; Cheng, Chun-Yen; Riolo, Jon V; Cree, Bruce Ac

Long-term safety and efficacy of ozanimod in relapsing multiple sclerosis: Final analysis of the DAYBREAK open-label extension trial

奥扎尼莫德治疗复发型多发性硬化症的长期安全性和有效性:DAYBREAK开放标签扩展试验的最终分析

Selmaj, Krzysztof W; Steinman, Lawrence; Comi, Giancarlo; Bar-Or, Amit; Arnold, Douglas L; Hartung, Hans-Peter; Montalbán, Xavier; Havrdová, Eva K; Sheffield, James K; Krakovich, Anthony; Cheng, Chun-Yen; Riolo, Jon V; Pachai, Chahin; Thorpe, Andrew; DeBoer, Erik; Kappos, Ludwig; Cohen, Jeffrey A; Cree, Bruce Ac

Five-Year Safety and Efficacy Outcomes with Ofatumumab in Patients with Relapsing Multiple Sclerosis

奥法妥木单抗治疗复发型多发性硬化症患者的五年安全性和有效性结果

Hauser, Stephen L; Cohen, Jeffrey A; de Sèze, Jérôme; Meuth, Sven G; Giacomini, Paul S; Nakahara, Jin; Oreja-Guevara, Celia; Robertson, Derrick; Wray, Sibyl; Bhatt, Alit; Hu, Xixi; Xi, Jing; Piccolo, Rebecca; Jehl, Valentine; Sullivan, Roseanne; Boer, Ibolya; Wiendl, Heinz; Kappos, Ludwig