Antisense oligonucleotides extend survival and reverse decrement in muscle response in ALS models
反义寡核苷酸可延长ALS模型中的生存期并逆转肌肉反应减弱。
期刊:Journal of Clinical Investigation
影响因子:13.6
doi:10.1172/JCI99081
McCampbell, Alex; Cole, Tracy; Wegener, Amy J; Tomassy, Giulio S; Setnicka, Amy; Farley, Brandon J; Schoch, Kathleen M; Hoye, Mariah L; Shabsovich, Mark; Sun, Linhong; Luo, Yi; Zhang, Mingdi; Comfort, Nicole; Wang, Bin; Amacker, Jessica; Thankamony, Sai; Salzman, David W; Cudkowicz, Merit; Graham, Danielle L; Bennett, C Frank; Kordasiewicz, Holly B; Swayze, Eric E; Miller, Timothy M