Homology-driven genome editing in hematopoietic stem and progenitor cells using ZFN mRNA and AAV6 donors
使用 ZFN mRNA 和 AAV6 供体在造血干细胞和祖细胞中进行同源性驱动的基因组编辑
期刊:Nature Biotechnology
影响因子:33.1
doi:10.1038/nbt.3408
Jianbin Wang, Colin M Exline, Joshua J DeClercq, G Nicholas Llewellyn, Samuel B Hayward, Patrick Wai-Lun Li, David A Shivak, Richard T Surosky, Philip D Gregory, Michael C Holmes, Paula M Cannon