The definition of neuronopathic Gaucher disease
神经病变型戈谢病的定义
期刊:Journal of Inherited Metabolic Disease
影响因子:3.8
doi:10.1002/jimd.12235
Schiffmann, Raphael; Sevigny, Jeff; Rolfs, Arndt; Davies, Elin Haf; Goker-Alpan, Ozlem; Abdelwahab, Magy; Vellodi, Ashok; Mengel, Eugen; Lukina, Elena; Yoo, Han-Wook; Collin-Histed, Tanya; Narita, Aya; Dinur, Tama; Revel-Vilk, Shoshana; Arkadir, David; Szer, Jeff; Wajnrajch, Michael; Ramaswami, Uma; Sidransky, Ellen; Donald, Aimee; Zimran, Ari