日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Application of in-vitro-cultured primary hepatocytes to evaluate species translatability and AAV transduction mechanisms of action.

应用体外培养的原代肝细胞评估物种转化性和 AAV 转导作用机制

Liu Su, Razon Lisa, Ritchie Olivia, Sihn Choong-Ryoul, Handyside Britta, Berguig Geoffrey, Woloszynek Jill, Zhang Lening, Batty Paul, Lillicrap David, Agrawal Vishal, Cortesio Christa, Gebretsadik Kahsay, Akeefe Hassibullah, Colosi Peter, Kim Benjamin, Bunting Stuart, Fong Sylvia

Christian Personalism versus Utilitarianism: An Analysis of Their Approaches to Love and Suffering

基督教人格主义与功利主义:对二者在爱与苦难观上的分析

Colosi, Peter J

Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery

用于治疗X连锁视网膜劈裂症的视网膜AAV8-RS1基因疗法:玻璃体内注射I/IIa期临床试验的初步结果

Cukras, Catherine; Wiley, Henry E; Jeffrey, Brett G; Sen, H Nida; Turriff, Amy; Zeng, Yong; Vijayasarathy, Camasamudram; Marangoni, Dario; Ziccardi, Lucia; Kjellstrom, Sten; Park, Tae Kwon; Hiriyanna, Suja; Wright, J Fraser; Colosi, Peter; Wu, Zhijian; Bush, Ronald A; Wei, Lisa L; Sieving, Paul A

Preclinical Dose-Escalation Study of Intravitreal AAV-RS1 Gene Therapy in a Mouse Model of X-linked Retinoschisis: Dose-Dependent Expression and Improved Retinal Structure and Function

在X连锁视网膜劈裂症小鼠模型中,玻璃体内注射AAV-RS1基因疗法的临床前剂量递增研究:剂量依赖性表达及视网膜结构和功能的改善

Bush, Ronald A; Zeng, Yong; Colosi, Peter; Kjellstrom, Sten; Hiriyanna, Suja; Vijayasarathy, Camasamudram; Santos, Maria; Li, Jinbo; Wu, Zhijian; Sieving, Paul A

A long-term efficacy study of gene replacement therapy for RPGR-associated retinal degeneration

基因替代疗法治疗RPGR相关视网膜变性的长期疗效研究

Wu, Zhijian; Hiriyanna, Suja; Qian, Haohua; Mookherjee, Suddhasil; Campos, Maria M; Gao, Chun; Fariss, Robert; Sieving, Paul A; Li, Tiansen; Colosi, Peter; Swaroop, Anand

Preclinical safety evaluation of a recombinant AAV8 vector for X-linked retinoschisis after intravitreal administration in rabbits

重组AAV8载体治疗X连锁视网膜劈裂症的临床前安全性评价(兔玻璃体内注射)

Marangoni, Dario; Wu, Zhijian; Wiley, Henry E; Zeiss, Caroline J; Vijayasarathy, Camasamudram; Zeng, Yong; Hiriyanna, Suja; Bush, Ronald A; Wei, Lisa L; Colosi, Peter; Sieving, Paul A

Laser photocoagulation enhances adeno-associated viral vector transduction of mouse retina.

激光光凝可增强腺相关病毒载体对小鼠视网膜的转导作用

Lee Si Hyung, Colosi Peter, Lee Heuiran, Ohn Young-Hoon, Kim Sung-Woon, Kwak Hyung Woo, Park Tae Kwann

Effect of genome size on AAV vector packaging

基因组大小对AAV载体包装的影响

Wu, Zhijian; Yang, Hongyan; Colosi, Peter

PDGF-CC blockade inhibits pathological angiogenesis by acting on multiple cellular and molecular targets

PDGF-CC阻断通过作用于多个细胞和分子靶点来抑制病理性血管生成。

Hou, Xu; Kumar, Anil; Lee, Chunsik; Wang, Bin; Arjunan, Pachiappan; Dong, Lijin; Maminishkis, Arvydas; Tang, Zhongshu; Li, Yang; Zhang, Fan; Zhang, Shi-Zhuang; Wardega, Piotr; Chakrabarty, Sagarika; Liu, Baoying; Wu, Zhijian; Colosi, Peter; Fariss, Robert N; Lennartsson, Johan; Nussenblatt, Robert; Gutkind, J Silvio; Cao, Yihai; Li, Xuri

Mutations on the external surfaces of adeno-associated virus type 2 capsids that affect transduction and neutralization

影响转导和中和的腺相关病毒2型衣壳外表面突变

Lochrie, Michael A; Tatsuno, Gwen P; Christie, Brian; McDonnell, Jennifer Wellman; Zhou, Shangzhen; Surosky, Richard; Pierce, Glenn F; Colosi, Peter