Preclinical toxicology and biodistribution studies of recombinant adeno-associated virus 1 human acid α-glucosidase
重组腺相关病毒1型人酸性α-葡萄糖苷酶的临床前毒理学和生物分布研究
期刊:Human Gene Therapy Clinical Development
影响因子:
doi:10.1089/humc.2013.147
Conlon, Thomas J; Erger, Kirsten; Porvasnik, Stacy; Cossette, Travis; Roberts, Cheryl; Combee, Lynn; Islam, Saleem; Kelley, Jeffry; Cloutier, Denise; Clément, Nathalie; Abernathy, Corinne R; Byrne, Barry J