Drugs Repurposing of Molecules Modulating Human Delta Globin Gene Expression via a Model of Transgenic Foetal Liver Cells: Implications for Beta-Hemoglobinopathy Therapeutics.
通过转基因胎肝细胞模型对调节人类δ珠蛋白基因表达的分子进行药物再利用:对β-血红蛋白病治疗的意义
期刊:Biomolecules
影响因子:4.8
doi:10.3390/biom15040565
Simbula Michela, Manchinu Maria Francesca, Olla Stefania, Congiu Michela, Vaccargiu Simona, Caria Cristian Antonio, Poddie Daniela, Ristaldi Maria Serafina