日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Mapping PTBP2 binding in human brain identifies SYNGAP1 as a target for therapeutic splice switching

通过绘制人脑中 PTBP2 的结合图谱,确定 SYNGAP1 是治疗性剪接转换的靶点。

Jennine M Dawicki-McKenna # ,Alex J Felix # ,Elisa A Waxman ,Congsheng Cheng ,Defne A Amado ,Paul T Ranum ,Alexey Bogush ,Lea V Dungan ,Jean Ann Maguire ,Alyssa L Gagne ,Elizabeth A Heller ,Deborah L French ,Beverly L Davidson ,Benjamin L Prosser

High-fidelity SaCas9 identified by directional screening in human cells

通过人类细胞中的定向筛选鉴定出高保真度SaCas9

Haihua Xie, Xianglian Ge, Fayu Yang, Bang Wang, Shuang Li, Jinzhi Duan, Xiujuan Lv, Congsheng Cheng, Zongming Song, Changbao Liu, Junzhao Zhao, Yu Zhang, Jinyu Wu, Caixia Gao, Jinwei Zhang, Feng Gu

The long non-coding RNA NEAT1 is elevated in polyglutamine repeat expansion diseases and protects from disease gene-dependent toxicities

长链非编码RNA NEAT1在多聚谷氨酰胺重复序列扩增疾病中表达升高,并能保护机体免受疾病基因依赖性毒性的影响。

Congsheng Cheng ,Ryan M Spengler ,Megan S Keiser ,Alejandro Mas Monteys ,Julianne M Rieders ,Shyam Ramachandran ,Beverly L Davidson