Context base editing for splice correction of IVSI-110 β-thalassemia
用于 IVSI-110 β-地中海贫血剪接校正的上下文库编辑
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2024.102183
Basma Naiisseh, Panayiota L Papasavva, Nikoletta Y Papaioannou, Marios Tomazou, Lola Koniali, Xenia Felekis, Constantina G Constantinou, Maria Sitarou, Soteroula Christou, Marina Kleanthous, Carsten W Lederer, Petros Patsali