日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

An integrated enzymatic and computational pipeline for quantifying off-target base-editing.

用于量化脱靶碱基编辑的集成酶学和计算流程

McFarland Alexander G, Ooi Soon-Keat, Tafuri Davin, Kamali Elahe, Cooper Natalie, Cook Emma J, Reddy Shantan, Jarocha Danuta, Wellhausen Nils, Gill Saar I, Roche Aoife M, Fraietta Joseph A, Bushman Frederic D, Herbst Friederike

Biodiversity impacts of the 2019-2020 Australian megafires

2019-2020年澳大利亚特大火灾对生物多样性的影响

Driscoll, Don A; Macdonald, Kristina J; Gibson, Rebecca K; Doherty, Tim S; Nimmo, Dale G; Nolan, Rachael H; Ritchie, Euan G; Williamson, Grant J; Heard, Geoffrey W; Tasker, Elizabeth M; Bilney, Rohan; Porch, Nick; Collett, Rachael A; Crates, Ross A; Hewitt, Alison C; Pendall, Elise; Boer, Matthias M; Gates, Jody; Boulton, Rebecca L; Mclean, Christopher M; Groffen, Heidi; Maisey, Alex C; Beranek, Chad T; Ryan, Shelby A; Callen, Alex; Hamer, Andrew J; Stauber, Andrew; Daly, Garry J; Gould, John; Klop-Toker, Kaya L; Mahony, Michael J; Kelly, Oliver W; Wallace, Samantha L; Stock, Sarah E; Weston, Christopher J; Volkova, Liubov; Black, Dennis; Gibb, Heloise; Grubb, Joshua J; McGeoch, Melodie A; Murphy, Nick P; Lee, Joshua S; Dickman, Chris R; Neldner, Victor J; Ngugi, Michael R; Miritis, Vivianna; Köhler, Frank; Perri, Marc; Denham, Andrew J; Mackenzie, Berin D E; Reid, Chris A M; Rayment, Julia T; Arriaga-Jiménez, Alfonsina; Hewins, Michael W; Hicks, Andrew; Melbourne, Brett A; Davies, Kendi F; Bitters, Matthew E; Linley, Grant D; Greenville, Aaron C; Webb, Jonathan K; Roberts, Bridget; Letnic, Mike; Price, Owen F; Walker, Zac C; Murray, Brad R; Verhoeven, Elise M; Thomsen, Alexandria M; Keith, David; Lemmon, Jedda S; Ooi, Mark K J; Allen, Vanessa L; Decker, Orsi T; Green, Peter T; Moussalli, Adnan; Foon, Junn K; Bryant, David B; Walker, Ken L; Bruce, Matthew J; Madani, George; Tscharke, Jeremy L; Wagner, Benjamin; Nitschke, Craig R; Gosper, Carl R; Yates, Colin J; Dillon, Rebecca; Barrett, Sarah; Spencer, Emma E; Wardle, Glenda M; Newsome, Thomas M; Pulsford, Stephanie A; Singh, Anu; Roff, Adam; Marsh, Karen J; Mcdonald, Kye; Howell, Lachlan G; Lane, Murraya R; Cristescu, Romane H; Witt, Ryan R; Cook, Emma J; Grant, Felicity; Law, Bradley S; Seddon, Julian; Berris, Karleah K; Shofner, Ryan M; Barth, Mike; Welz, Torran; Foster, Alison; Hancock, David; Beitzel, Matthew; Tan, Laura X L; Waddell, Nathan A; Fallow, Pamela M; Schweickle, Laura; Le Breton, Tom D; Dunne, Craig; Green, Mikayla; Gilpin, Amy-Marie; Cook, James M; Power, Sally A; Hogendoorn, Katja; Brawata, Renee; Jolly, Chris J; Tozer, Mark; Reiter, Noushka; Phillips, Ryan D

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

利用靶向造血干细胞的脂质纳米颗粒构建致死性α-地中海贫血小鼠模型,并通过慢病毒基因治疗进行治疗。

Chappell, Maxwell E; Breda, Laura; Tricoli, Lucas; Guerra, Amaliris; Jarocha, Danuta; Castruccio Castracani, Carlo; Papp, Tyler E; Tanaka, Naoto; Hamilton, Nolan; Triebwasser, Michael P; Ghiaccio, Valentina; Fedorky, Megan T; Gollomp, Kandace L; Bochenek, Veronica; Roche, Aoife M; Everett, John K; Cook, Emma J; Bushman, Frederic D; Teawtrakul, Nattiya; Glentis, Stavros; Kattamis, Antonis; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Abdulmalik, Osheiza; Parhiz, Hamideh; Rivella, Stefano