日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial

在伴有预先存在的腺相关病毒5型中和抗体的B型血友病患者中应用依曲那康基因(Etranacogene dezaparvovec):HOPE-B试验的4年亚组结果

Klamroth, Robert; Monahan, Paul E; Van der Valk, Paul; Quon, Doris; Kazmi, Rashid Saeed; Coppens, Michiel; O'Connell, Niamh; Pipe, Steven W; von Drygalski, Annette; Afzal, Saira; Gabriel, Richard; Youssar, Loubna; Gill, Sean; Jansen, Nathalie; Wang, Fei; Le Quellec, Sandra; Hermans, Cedric

Health care resources and costs associated with delivering gene therapy for hemophilia in clinical practice

在临床实践中,为血友病患者提供基因治疗所涉及的医疗资源和成本

Prameyllawati, Diaz M; Mussert, Caroline M A; Oude Voshaar, Martijn A H; Lingsma, Hester F; Cnossen, Marjon H; Coppens, Michiel; Meijer, Karina; van der Valk, Paul R; Leebeek, Frank W G; Ten Ham, Renske M T

Systematic review update of organisational-level mental health promotion interventions: evidence from healthcare, construction, and telework-based mobile work settings

组织层面心理健康促进干预措施的系统评价更新:来自医疗保健、建筑业和远程办公移动工作环境的证据

Giovanis, Eleftherios; Ozdamar, Oznur; Aust, Birgit; Cresswell-Smith, Johanna; Pashoja, Arlinda Cerga; Leduc, Caleb; Sinesi, Andrea; Piña, Carolina; Van Audenhove, Chantal; Qirjako, Gentiana; Ross, Victoria; Kenneally, Margaret; Reich, Hanna; Coppens, Evelien; da Conceição, Virgínia; Torner, Helena Pardina; Mustafa, Sevim; Purebl, György; O'Connor, Ainslie; Bücker, Joana; Riva, Silvia; Seyen, Alexandra Perez T; Arensman, Ella; Lobo, Pedro

Pathogenic UNC13A variants cause a neurodevelopmental syndrome by impairing synaptic function

致病性UNC13A变异体通过损害突触功能导致神经发育综合征。

Asadollahi, Reza; Ahmad, Aisha; Boonsawat, Paranchai; Shahanoor Hinzen, Jasmine; Lohse, Mareike; Bouazza-Arostegui, Boris; Sun, Siqi; Utesch, Tillmann; Sommer, Jonas D; Ilic, Dragana; Padmanarayana, Murugesh; Fischermanns, Kati; Ranjan, Mrinalini; Boll, Moritz; Ka, Chandran; Piton, Amélie; Mattioli, Francesca; Isidor, Bertrand; Õunap, Katrin; Reinson, Karit; Wojcik, Monica H; Marshall, Christian R; Mercimek-Andrews, Saadet; Matsumoto, Naomichi; Miyake, Noriko; Stephan, Bruno de Oliveira; Honjo, Rachel Sayuri; Bertola, Debora R; Kim, Chong Ae; Yusupov, Roman; Mefford, Heather C; Christodoulou, John; Lee, Joy; Heath, Oliver; Brown, Natasha J; Baker, Naomi; Stark, Zornitza; Delatycki, Martin; Lake, Nicole J; Zeidler, Shimriet; Zuurbier, Linda; Maas, Saskia M; de Kruiff, Chris C; Rajabi, Farrah; Rodan, Lance H; Coury, Stephanie A; Platzer, Konrad; Oppermann, Henry; Abou Jamra, Rami; Beblo, Skadi; Maxton, Caroline; Śmigiel, Robert; Underhill, Hunter; Dubbs, Holly; Rosen, Alyssa; Helbig, Katherine L; Helbig, Ingo; Ruggiero, Sarah McKeown; Fitzgerald, Mark P; Kraemer, Dennis; Prada, Carlos E; Tenney, Jeffrey; Jayakar, Parul; Redon, Sylvia; Lefranc, Jérémie; Uguen, Kevin; Race, Simone; Efthymiou, Stephanie; Maroofian, Reza; Houlden, Henry; Coppens, Sandra; Deconinck, Nicolas; Ashokkumar, Balasubramaniem; Varalakshmi, Perumal; Gowda K, Vykunta Raju; Eghbal, Fatemeh; Ghayoor Karimiani, Ehsan; Heidari, Morteza; Neidhardt, John; Owczarek-Lipska, Marta; Korenke, G Christoph; Bamshad, Michael J; Campeau, Philippe M; Lehman, Anna; Hendon, Laura G; Wentzensen, Ingrid M; Monaghan, Kristin G; Chen, Yanmin; Szuto, Anna; Cohn, Ronald D; Au, Ping Yee Billie; Hübner, Christoph; Boschann, Felix; Manickam, Kandamurugu; Koboldt, Daniel C; Rad, Aboulfazl; Oprea, Gabriela; Bachman, Kristine K; Seeley, Andrea H; Agolini, Emanuele; Terracciano, Alessandra; Carmelo, Piscopo; Bupp, Caleb; Grysko, Bethany; Rein-Rothschild, Annick; Ben Zeev, Bruria; Margolin, Amy; Morrison, Jennifer; Dagli, Aditi; Stolerman, Elliot; Louie, Raymond J; Washington, Camerun; Stevens, Servi J C; Heijligers, Malou; Alkuraya, Fowzan S; Lisfeld, Jasmin; Neu, Axel; Paoli Monteiro, Fabíola; Santos Pessoa, André Luiz; Camelo-Filho, Antonio Edvan; Kok, Fernando; Koeberl, Dwight; Riley, Kacie; Burglen, Lydie; Doummar, Diane; Héron, Bénédicte; Mignot, Cyril; Keren, Boris; Charles, Perrine; Nava, Caroline; Bernhard, Felix P; Kühn, Andrea A; Thoms, Sven; Morrie, Ryan D; Mekhoubad, Shila; Green, Eric M; Barmada, Sami J; Gitler, Aaron D; Jahn, Olaf; Rhee, Jeong Seop; Rosenmund, Christian; Mitkovski, Mišo; Sticht, Heinrich; Sun, Han; Le Gac, Gerald; Taschenberger, Holger; Brose, Nils; Dittman, Jeremy S; Rauch, Anita; Lipstein, Noa

High-resolution proteomics unveils salivary gland disruption and saliva-hemolymph protein exchange in Plasmodium-infected mosquitoes

高分辨率蛋白质组学揭示疟原虫感染蚊子唾液腺功能紊乱和唾液-血淋巴蛋白交换

Alves E Silva, Thiago Luiz; Kanatani, Sachi; Barletta Ferreira, Ana Beatriz; Schwartz, Cindi L; Liffner, Benjamin; Talyuli, Octavio A C; Olivas, Janet; Nagata, Bianca M; Pala, Zarna Rajeshkumar; Pascini, Tales; Alves, Derron A; Zhao, Ming; Suzuki, Motoshi; Dorner, Lilian P; Frischknecht, Friedrich; Coppens, Isabelle; Barillas-Mury, Carolina; Absalon, Sabrina; Ribeiro, Jose M C; Sinnis, Photini; Vega-Rodriguez, Joel

WorkflowHub: a registry for computational workflows

WorkflowHub:计算工作流注册表

Gustafsson, Ove Johan Ragnar; Wilkinson, Sean R; Bacall, Finn; Soiland-Reyes, Stian; Leo, Simone; Pireddu, Luca; Owen, Stuart; Juty, Nick; Fernández, José M; Brown, Tom; Ménager, Hervé; Grüning, Björn; Capella-Gutierrez, Salvador; Coppens, Frederik; Goble, Carole

Road Towards Ambulatory Colectomy: Patient Outcomes and Experience During a Feasibility Study

迈向门诊结肠切除术之路:可行性研究中的患者结局和体验

Coeckelberghs, Ellen; Wolthuis, Albert; Teunkens, An; Dewinter, Geertrui; Coppens, Steve; Van Langenhoven, Leen; Vanholzaets, Lotte; Pierrart, Julie; Schraepen, Cédric; Bislenghi, Gabriele; D'Hoore, André

Targeted Therapy for Complex Lymphatic Anomalies in Patients with Noonan Syndrome and Related Disorders

针对努南综合征及相关疾病患者复杂淋巴异常的靶向治疗

Leenders, Erika K S M; van den Brink, Vera C; Kleimeier, Lotte E R; Woutersen, Danielle T J; Coppens, Catelijne H; den Hertog, Jeroen; Klein, Willemijn M; Rinne, Tuula; Vrancken, Sabine L; de Wildt, Saskia N; Draaisma, Jos M T; Fuijkschot, Joris

Preclinical toxicological assessment of an α-galactosylceramide-adjuvanted mRNA cancer vaccine in Wistar Han rats and domestic pigs.

对Wistar Han大鼠和家猪进行α-半乳糖基神经酰胺佐剂mRNA癌症疫苗的临床前毒理学评估

Meulewaeter Sofie, De Velder Margo, Reckelbus Diethard, Mwangi Kevin, Ehouarne Thomas, Aernout Ilke, Engelen Yanou, Halimi Fellanza, Van Herteryck Isis, De Bels Lobke, Redant Valerie, De la Mane Louise, Ingels Joline, Coppens Bo, Van Calenbergh Serge, Cornillie Pieter, Holtappels Gabriële, Descamps Benedicte, Vanrompay Daisy, De Smedt Stefaan C, Van den Broeck Wim, Vandekerckhove Bart, Devreese Mathias, Verbeke Rein, Lentacker Ine

Comprehensive analysis of CNOT3-related neurodevelopmental disorders: phenotypic and genotypic characterization

CNOT3相关神经发育障碍的综合分析:表型和基因型特征

Engel, Camille; Rendek, Michaela; Assoumani, Jessica; Argilli, Emanuela; Ariani, Francesca; Avice-Denizet, Anne-Laude; Bijlsma, Emilia K; Blanc, Pierre; Bruno, Lucia Pia; Callewaert, Bert; Capra, Valeria; Carullo, Michele; Chesneau, Bertrand; Coppens, Sandra; Curry, Cynthia; Dale, Breanne; Dahlen, Eric; Delahaye-Duriez, Andrée; Denommé-Pichon, Anne-Sophie; Demeer, Bénédicte; Dvořáková, Lenka; Fischer, Jan; Geneviève, David; Giacomini, Thea; Handrup, Mette M; Heron, Delphine; Hüning, Irina; Iacomino, Michelle; Isidor, Bertrand; Keren, Boris; Kmoch, Stanislav; Koolen, David A; Kübler, Andrea; Laštůvková, Jana; Le, Carolyn; Levy, Jonathan; Rizzo, Caterina Lo; Maitz, Silvia; Marlin, Sandrine; Mignot, Cyril; Mirzaa, Ghayda; Nagel, Inga; Neuens, Sebastian; Nosková, Lenka; Pao, Emily; Pecková, Anna; Plaisancie, Julie; Porrmann, Joseph; Privitera, Flavia; Reis, André; Renieri, Alessandra; Rio, Marlène; Rippert, Alyssa; Ryba, Lukáš; Scala, Marcello; Schieving, Jolanda H; Sherr, Elliott H; Shuen, Andrew; Sidlow, Richard; Smol, Thomas; Soblet, Julie; Striano, Pasquale; Suri, Mohnish; Syryn, Hannes; Tran Mau-Them, Frédéric; Travessa, Andre M; Van Gils, Julien; Vasileiou, Georgia; Verseput, Jolijn J A; Vilain, Catheline; Vincent-Delorme, Catherine; Vyhnálková, Emílie; Wakeling, Emma L; Zacher, Pia; Zara, Federico; Kuentz, Paul; Piard, Juliette