日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

FLT201, a novel liver-directed AAV gene therapy candidate for Gaucher disease type 1.

FLT201 是一种新型的肝脏靶向 AAV 基因治疗候选药物,用于治疗 1 型戈谢病。

Comper Fabrizio, Miranda Carlos J, Liou Benjamin, Dodev Tihomir, Jeyakumar Jey M, Canavese Miriam, Cocita Clement, Khoshrou Khashayar, Tiscornia Gustavo, Chisari Elisa, Stotter Emmaline, Shehu Erald, Sridharan Sudharsan, Yu I-Mei, Pandya Jalpa, Khinder Jaminder, Northcott Natalie, Kalcheva Petya, Correia Samantha, Sun Ying, Dane Allison P, Sheridan Rose, Nathwani Amit C, Corbau Romuald

Nonclinical study of ixo-vec gene therapy for nAMD supports efficacy for a human dose of 6E10 vg/eye and staggered dosing of fellow eyes.

针对 nAMD 的 ixo-vec 基因疗法的非临床研究支持对人类每眼 6E10 vg 剂量和对另一只眼睛分阶段给药的疗效

Poulsen Kris, Hanna Kelly, Nieves Julio, Nguyen Ngoc, Sharma Pallavi, Grishanin Ruslan, Corbau Romu, Kiss Szilárd

Differences in wild-type- and R338L-tenase complex formation are at the root of R338L-factor IX assay discrepancies

野生型和R338L突变型凝血酶原酶复合物形成差异是R338L突变型凝血因子IX检测结果不一致的根本原因。

Foley, Jonathan H; Shehu, Erald; Riddell, Anne; Gray, Elaine; Goodale, Andrew; Yu, I-Mei; Verhoef, Daniël; Little, John; Shattock, Diane; Kitchen, Steve; Chowdary, Pratima; Corbau, Romuald; Nathwani, Amit C

Exposure of Mytilus galloprovincialis to Microplastics: Accumulation, Depuration and Evaluation of the Expression Levels of a Selection of Molecular Biomarkers

地中海贻贝暴露于微塑料:积累、净化及部分分子生物标志物表达水平的评估

Pizzurro, Federica; Nerone, Eliana; Ancora, Massimo; Di Domenico, Marco; Mincarelli, Luana Fiorella; Cammà, Cesare; Salini, Romolo; Di Renzo, Ludovica; Di Giacinto, Federica; Corbau, Corinne; Bokan, Itana; Ferri, Nicola; Recchi, Sara

UAVs for Structure-From-Motion Coastal Monitoring: A Case Study to Assess the Evolution of Embryo Dunes over a Two-Year Time Frame in the Po River Delta, Italy

利用无人机进行基于运动的结构海岸监测:以意大利波河三角洲两年内胚胎沙丘的演变为例

Taddia, Yuri; Corbau, Corinne; Zambello, Elena; Pellegrinelli, Alberto

Data for the analysis of willingness to pay for Italian beaches

用于分析人们为意大利海滩支付意愿的数据

Rodella, Ilaria; Madau, Fabio; Mazzanti, Massimiliano; Corbau, Corinne; Carboni, Donatella; Utizi, Kizzi; Simeoni, Umberto

1-((2,4-Dichlorophenethyl)Amino)-3-Phenoxypropan-2-ol Kills Pseudomonas aeruginosa through Extensive Membrane Damage

1-((2,4-二氯苯乙基)氨基)-3-苯氧基丙烷-2-醇通过广泛的膜损伤杀死铜绿假单胞菌

Valerie Defraine, Veerle Liebens, Evelien Loos, Toon Swings, Bram Weytjens, Carolina Fierro, Kathleen Marchal, Liam Sharkey, Alex J O'Neill, Romu Corbau, Arnaud Marchand, Patrick Chaltin, Maarten Fauvart, Jan Michiels

Identification of 1-((2,4-Dichlorophenethyl)Amino)-3-Phenoxypropan-2-ol, a Novel Antibacterial Compound Active against Persisters of Pseudomonas aeruginosa

鉴定出一种新型抗菌化合物 1-((2,4-二氯苯乙基)氨基)-3-苯氧基丙-2-醇,该化合物对铜绿假单胞菌的持久菌具有活性。

Liebens, Veerle; Defraine, Valerie; Knapen, Wouter; Swings, Toon; Beullens, Serge; Corbau, Romu; Marchand, Arnaud; Chaltin, Patrick; Fauvart, Maarten; Michiels, Jan

RNAi prevents and reverses phenotypes induced by mutant human ataxin-1

RNAi可预防和逆转突变型人类共济蛋白-1诱导的表型

Keiser, Megan S; Monteys, Alejandro Mas; Corbau, Romuald; Gonzalez-Alegre, Pedro; Davidson, Beverly L

Deep Sequencing Insights in Therapeutic shRNA Processing and siRNA Target Cleavage Precision

深度测序揭示治疗性shRNA加工和siRNA靶向切割的精确性

Denise, Hubert; Moschos, Sterghios A; Sidders, Benjamin; Burden, Frances; Perkins, Hannah; Carter, Nikki; Stroud, Tim; Kennedy, Michael; Fancy, Sally-Ann; Lapthorn, Cris; Lavender, Helen; Kinloch, Ross; Suhy, David; Corbau, Romu