日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A scalable and cGMP-compatible autologous organotypic cell therapy for Dystrophic Epidermolysis Bullosa

一种可扩展且与 cGMP 兼容的自体器官型细胞疗法,用于治疗营养不良性大疱性表皮松解症

Gernot Neumayer #, Jessica L Torkelson #, Shengdi Li #, Kelly McCarthy, Hanson H Zhen, Madhuri Vangipuram, Marius M Mader, Gulilat Gebeyehu, Taysir M Jaouni, Joanna Jacków-Malinowska, Avina Rami, Corey Hansen, Zongyou Guo, Sadhana Gaddam, Keri M Tate, Alberto Pappalardo, Lingjie Li, Grace M Chow, Ke

A scalable, GMP-compatible, autologous organotypic cell therapy for Dystrophic Epidermolysis Bullosa

一种可扩展、符合 GMP 标准的自体器官型细胞疗法,用于治疗营养不良性大疱性表皮松解症

Gernot Neumayer, Jessica L Torkelson, Shengdi Li, Kelly McCarthy, Hanson H Zhen, Madhuri Vangipuram, Joanna Jackow, Avina Rami, Corey Hansen, Zongyou Guo, Sadhana Gaddam, Alberto Pappalardo, Lingjie Li, Amber Cramer, Kevin R Roy, Thuylinh Michelle Nguyen, Koji Tanabe, Patrick S McGrath, Anna Bruckne

Engineering human skin model innervated with itch sensory neuron-like cells differentiated from induced pluripotent stem cells

由诱导性多能干细胞分化而来的瘙痒感觉神经元样细胞所支配的工程人体皮肤模型

Zongyou Guo, Chi-Kun Tong, Joanna Jacków, Yanne S Doucet, Hasan E Abaci, Wangyong Zeng, Corey Hansen, Ryota Hayashi, Dominick DeLorenzo, Avina Rami, Alberto Pappalardo, Ellen A Lumpkin, Angela M Christiano

CRISPR/Cas9-based targeted genome editing for correction of recessive dystrophic epidermolysis bullosa using iPS cells

基于 CRISPR/Cas9 的靶向基因组编辑,利用 iPS 细胞矫正隐性营养不良型大疱性表皮松解症

Joanna Jacków, Zongyou Guo, Corey Hansen, Hasan E Abaci, Yanne S Doucet, Jung U Shin, Ryota Hayashi, Dominick DeLorenzo, Yudai Kabata, Satoru Shinkuma, Julio C Salas-Alanis, Angela M Christiano