Transplantation of Wild-Type Hematopoietic Stem and Progenitor Cells Improves Disease Phenotypes in a Mucopolysaccharidosis IIIC Mouse Model.
移植野生型造血干细胞和祖细胞可改善粘多糖贮积症 IIIC 小鼠模型的疾病表型
期刊:Cell Transplantation
影响因子:3.2
doi:10.1177/09636897251323966
Badell-Grau Rafael A, Pakravesh Kasra, Thai Kevin Eric, Son Frankie, Chen Rola, Rainaldi Joseph, Duong Kalvin, Losay Pauline, Sivakumar Anusha, Khare Veenita, Corl Alexis N, Pithia Rushil, Tran Christine, Esko Jefferey D, Cherqui Stephanie