日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy (OTL-203) for Hurler syndrome

造血干细胞和祖细胞基因治疗(OTL-203)治疗赫勒综合征的非神经系统、非骨骼结局

Tucci, Francesca; Uria Oficialdegui, M Luz; Consiglieri, Giulia; Cossutta, Matilde; Filisetti, Chiara; Fumagalli, Francesca; Butera, Carla; Santangelo, Roberto; Colombo, Michele; Manitto, Maria Pia; Stoppani, Monica; Martina, Elisabetta; Danè, Giulia; Camesasca, Chiara; Risca, Giulia; De Pellegrin, Maurizio; Scarparo, Stefano; Sarzana, Marina; Puricelli, Cristina; Galimberti, Stefania; Darin, Silvia; Silvani, Paolo; Bonanomi, Sonia; Gasperini, Serena; Naldini, Luigi; Gentner, Bernhard; Parini, Rossella; Del Toro, Mireia; Diaz-de-Heredia, Cristina; Aiuti, Alessandro; Bernardo, Maria Ester

Development and characterization of a model of mucopolysaccharidosis type IVA for evaluating therapies targeting bone disease

建立和表征IVA型粘多糖贮积症模型,用于评估针对骨骼疾病的疗法

Berti, Margherita; Ceriotti, Selene; Santi, Ludovica; Alberti, Gaia; Beretta, Stefano; Degl'Innocenti, Sara; Ruatti, Cristina; Savoia, Evelyn Oliva; Jofra-Hernandez, Raisa; De Ponti, Giada; Bolamperti, Simona; Villa, Isabella; Galeotti, Fabio; Romano, Alessandro; Visigalli, Ilaria; Norata, Rossana; Rocchi, Martina; Cristofori, Patrizia; Cossutta, Matilde; Consiglieri, Giulia; Tucci, Francesca; Santorelli, Lucia; Grumati, Paolo; Ronfani, Lorenza; D'Adamo, Patrizia; Giustina, Andrea; Angelozzi, Marco; Settembre, Carmine; Mortellaro, Alessandra; Scala, Serena; Sanvito, Francesca; Volpi, Nicola; Aiuti, Alessandro; Bernardo, Maria Ester; Crippa, Stefania

New standards in HER2-low testing: the CASI-01 comparative methods study

HER2低表达检测的新标准:CASI-01比较方法研究

Dabbs, David J; Torlakovic, Emina; Nielsen, Søren; Parry, Suzanne C; Yu, Jing; Stoos, Catherine; Clark, Beth; Høeg, Henrik; Thagaard, Jeppe; Sompuram, Seshi R; Naber, Stephen P; Yagi, Yukako; Sayre, James; Vani, Kodela; Cossutta, Mélissande; Soussaline, Francoise; Papine, Alexandre; t'Hart, Nils A; Szabolcs, Matthias J; Jasani, Bharat; Kinloch, Mary; Chiriboga, Luis; Miller, Keith; Bogen, Steve

Ultrasonographic hip morphology in mucopolysaccharidosis type I Hurler after hematopoietic stem cell gene therapy

造血干细胞基因治疗后I型粘多糖贮积症Hurler综合征患者的髋关节超声形态

De Pellegrin, Maurizio; Filisetti, Chiara; Cossutta, Matilde; Colombo, Michele; Consiglieri, Giulia; Tucci, Francesca; Aiuti, Alessandro; Bernardo, Maria Ester

S149: OTHER MALIGNANCIES IN THE HISTORY OF CLL: THE FINAL ANALYSIS OF THE INTERNATIONAL MULTICENTER STUDY CONDUCTED BY ERIC, IN HARMONY

S149:慢性淋巴细胞白血病病史中的其他恶性肿瘤:ERIC 和 IN HARMONY 开展的国际多中心研究的最终分析

Tucci, Francesca; Consiglieri, Giulia; Cossutta, Matilde; Bernardo, Maria Ester; Chatzikonstantinou, Thomas; Scarfò, Lydia; Karakatsoulis, Georgios; Minga, Eva; Chamou, Dimitra; Iacoboni, Gloria; Kotaskova, Jana; Demosthenous, Christos; Alcoceba, Miguel; Al-Shemari, Salem; Aurran-Schleinitz, Thérèse; Bacchiarri, Francesca; Bellido, Mar; Bijou, Fontanet; Calleja, Anne; Medina, Angeles; Khan, Mehreen Ali; Cassin, Ramona; Chatzileontiadou, Sofia; Collado, Rosa; Davis, Zadie; Dimou, Maria; Donaldson, David; Santos, Gimena Dos; Dreta, Barbara; Efstathopoulou, Maria; El-Ashwah, Shaimaa; Enrico, Alicia; Fresa, Alberto; Galimberti, Sara; Galitzia, Andrea; García-Serra, Rocío; Gimeno, Eva; González-Gascón-Y-Marín, Isabel; Gozzetti, Alessandro; Guarente, Valerio; Guieze, Romain; Gogia, Ajay; Gupta, Ritu; Harrop, Sean; Hatzimichael, Eleftheria; Herishanu, Yair; Hernández-Rivas, José-Ángel; Inchiappa, Luca; Jaksic, Ozren; Janssen, Susanne; Kalicińska, Elżbieta; Kamel, Laribi; Karakus, Volkan; Kater, Arnon P; Kho, Bonnie; Kislova, Maria; Konstantinou, Εliana; Koren-Michowitz, Maya; Kotsianidis, Ioannis; Kreitman, Robert J; Labrador, Jorge; Lad, Deepesh; Levin, Mark-David; Levy, Ilana; Longval, Thomas; Lopez-Garcia, Alberto; Marquet, Juan; Maynadié, Marc; Maslejova, Stanislava; Mayor-Bastida, Carlota; Mihaljevic, Biljana; Milosevic, Ivana; Miras, Fatima; Moia, Riccardo; Morawska, Marta; Murru, Roberta; Nath, Uttam Kumar; Navarro-Bailón, Almudena; Oliveira, Ana C; Olivieri, Jacopo; Oscier, David; Panovska-Stavridis, Irina; Papaioannou, Maria; Papajík, Tomas; Phumphukhieo, Punyarat; Pierie, Cheyenne; Puiggros, Anna; Rani, Lata; Reda, Gianluigi; Rigolin, Gian Matteo; Ronson, Aharon; Ruchlemer, Rosa; de Deus Santos, Marcos Daniel; Schipani, Mattia; Schiwitza, Annett; Shen, Yandong; Simkovic, Martin; Smirnova, Svetlana; Sameh Abdelrahman Soliman, Dina; Spacek, Martin; Tadmor, Tamar; Tomic, Kristina; Tse, Eric; Vassilakopoulos, Theodoros; Visentin, Andrea; Vitale, Candida; von Tresckow, Julia; Vrachiolias, George; Vukovic, Vojin; Walewska, Renata; Wasik-Szczepanek, Ewa; Xu, Zhenshu; Yagci, Munci; Yañez, Lucrecia; Yassin, Mohamed; Zuchnicka, Jana; Angelopoulou, Maria; Antic, Darko; Biderman, Bella; Catherwood, Mark; Claus, Rainer; Coscia, Marta; Cuneo, Antonio; Demirkan, Fatih; Espinet, Blanca; Gaidano, Gianluca; Kalashnikova, Olga; Laurenti, Luca; Nikitin, Eugene; Pangalis, Gerassimos A; Panagiotidis, Panagiotis; Mulligan, Stephen; Popov, Viola Maria; Pospisilova, Sarka; Smolej, Lukas; Sportoletti, Paolo; Stavroyianni, Niki; Tam, Constantine; Trentin, Livio; Chatzidimitriou, Anastasia; Bosch, Francesc; Doubek, Michael; Ghia, Paolo; Stamatopoulos, Kostas

Inflammatory status in pediatric sickle cell disease: Unravelling the role of immune cell subsets

儿童镰状细胞病中的炎症状态:揭示免疫细胞亚群的作用

Silvio Marchesani ,Valentina Bertaina ,Olivia Marini ,Matilde Cossutta ,Margherita Di Mauro ,Gioacchino Andrea Rotulo ,Paolo Palma ,Letizia Sabatini ,Maria Isabella Petrone ,Giacomo Frati ,Giulia Monteleone ,Giuseppe Palumbo ,Giulia Ceglie

Industry payments to family medicine residents in Portugal: a descriptive analysis of the national transparency database

葡萄牙家庭医学住院医师的行业支付:国家透明度数据库的描述性分析

Ruivo, Marta; Cossutta, Fabrizio; Moreira Fonseca, Nuno

The blood count as a compass to navigate in the ever-changing landscape of the carrier state of hemoglobinopathies: a single-center Italian experience

血细胞计数如同指南针,引领我们应对不断变化的血红蛋白病携带者状态:意大利单中心经验

Marchesani, Silvio; Di Mauro, Margherita; Ceglie, Giulia; Grassia, Ginevra; Carletti, Michaela; Cristofaro, Rosa Carmela; Cossutta, Matilde; Curcio, Cristina; Palumbo, Giuseppe

Nucleolin Therapeutic Targeting Decreases Pancreatic Cancer Immunosuppression

核仁素治疗靶向降低胰腺癌免疫抑制

Matteo Ponzo, Anais Debesset, Mélissande Cossutta, Mounira Chalabi-Dchar, Claire Houppe, Caroline Pilon, Alba Nicolas-Boluda, Sylvain Meunier, Fabio Raineri, Allan Thiolat, Rémy Nicolle, Federica Maione, Serena Brundu, Carina Florina Cojocaru, Philippe Bouvet, Corinne Bousquet, Florence Gazeau, Chri

Nucleolin Targeting by N6L Inhibits Wnt/β-Catenin Pathway Activation in Pancreatic Ductal Adenocarcinoma

N6L 靶向核仁素可抑制胰腺导管腺癌中的 Wnt/β-Catenin 通路激活

Fabio Raineri, Sandrine Bourgoin-Voillard, Mélissande Cossutta, Damien Habert, Matteo Ponzo, Claire Houppe, Benoît Vallée, Michele Boniotto, Mounira Chalabi-Dchar, Philippe Bouvet, Anne Couvelard, Jerome Cros, Anais Debesset, José L Cohen, José Courty, Ilaria Cascone