日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Inhaled DNAI1 mRNA therapy for treatment of primary ciliary dyskinesia.

吸入式 DNAI1 mRNA 疗法治疗原发性纤毛运动障碍

Hennig Mirko, Bhattacharjee Rumpa B, Agarwal Ishita, Alfaifi Ali, Casillas Jade E, Chavez Sofia, Ishimaru Daniella, Liston David, Mohapatra Sakya, Molla Touhidul, Pathare Suyog, Sidhu Maninder S, Wang Peng, Wang Zechen, Lombana T Noelle, Kharitonov Vladimir G, Couch Jessica A, Lockhart David J, Wustman Brandon A

A Phase 1 study of GDC-0134, a dual leucine zipper kinase inhibitor, in ALS

一项针对肌萎缩侧索硬化症(ALS)的GDC-0134(一种双重亮氨酸拉链激酶抑制剂)的I期研究

Katz, Jonathan S; Rothstein, Jeffrey D; Cudkowicz, Merit E; Genge, Angela; Oskarsson, Björn; Hains, Avis B; Chen, Chen; Galanter, Joshua; Burgess, Braydon L; Cho, William; Kerchner, Geoffrey A; Yeh, Felix L; Ghosh, Arundhati Sengupta; Cheeti, Sravanthi; Brooks, Logan; Honigberg, Lee; Couch, Jessica A; Rothenberg, Michael E; Brunstein, Flavia; Sharma, Khema R; van den Berg, Leonard; Berry, James D; Glass, Jonathan D

Preexisting Antibodies to an F(ab')2 Antibody Therapeutic and Novel Method for Immunogenicity Assessment

针对F(ab')2抗体的预存抗体:一种新型的治疗性免疫原性评估方法

Ruppel, Jane; Brady, Ann; Elliott, Rebecca; Leddy, Cecilia; Palencia, Marco; Coleman, Daniel; Couch, Jessica A; Wakshull, Eric

Enhanced activation of reward mediating prefrontal regions in response to food stimuli in Prader-Willi syndrome

普拉德-威利综合征患者对食物刺激的奖赏介导前额叶区域的激活增强

Miller, Jennifer L; James, G Andrew; Goldstone, Anthony P; Couch, Jessica A; He, Guojun; Driscoll, Daniel J; Liu, Yijun