Adeno-Associated Virus-Mediated Gene Therapy in the Mashlool, Atp1a3Mashl/+, Mouse Model of Alternating Hemiplegia of Childhood
腺相关病毒介导的 Mashlool、Atp1a3Mashl/+ 儿童交替性偏瘫小鼠模型基因治疗
期刊:Human Gene Therapy
影响因子:3.9
doi:10.1089/hum.2020.191
Arsen S Hunanyan, Boris Kantor, Ram S Puranam, Courtney Elliott, Angela McCall, Justin Dhindsa, Promila Pagadala, Keri Wallace, Jordan Poe, Talha Gunduz, Aravind Asokan, Dwight D Koeberl, Mai K ElMallah, Mohamad A Mikati