日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Elexacaftor/Tezacaftor/Ivacaftor for Cystic Fibrosis and Rare CFTR Variants: In Vitro Translation to a Phase 3, Double-Blind, Randomized, Placebo-controlled Trial and Real-World Study

Elexacaftor/Tezacaftor/Ivacaftor 用于囊性纤维化和罕见 CFTR 变异:体外研究向 3 期双盲、随机、安慰剂对照试验和真实世界研究的转化

Castellani, Carlo; Mondejar-Lopez, Pedro; Van Goor, Fredrick; Quon, Bradley S; Alghisi, Federico; Fabrizzi, Benedetta; Ramsey, Bonnie; Taylor-Cousar, Jennifer L; McKone, Edward F; Tullis, Elizabeth; Weinstock, Tanya G; Tan, Vincent; Ahluwalia, Neil; Mahic, Milada; Liu, Lingyun; Saayman, Sheena; Altshuler, David; Waltz, David; Mall, Marcus A; Fajac, Isabelle

Long-term reductions in inflammation in people with cystic fibrosis treated with elexacaftor/tezacaftor/ivacaftor

使用 elexacaftor/tezacaftor/ivacaftor 治疗囊性纤维化患者可长期降低炎症水平

Sagel, Scott D; Poore, T Spencer; Wagner, Brandie D; Xie, Jing; Heltshe, Sonya L; Cross, Mary; Bratcher, Preston E; Taylor-Cousar, Jennifer L; Wilson, Alexandra; McBennett, Kimberly; Morgan, Sarah J; Singh, Pradeep K; Nichols, David P; Kelly, Andrea; Solomon, George M

Liver cirrhosis among females with cystic fibrosis using hormonal contraception

使用激素避孕的囊性纤维化女性发生肝硬化

Chin, Jennifer; Sarkar, Monika; Magaret, Amalia S; Hsu, Chialing; West, Natalie; Walker, Patricia; Langfelder-Schwind, Elinor; Taylor-Cousar, Jennifer L; Ladores-Barrett, Sigrid; Hadijiliadis, Denis; Roe, Andrea H; Uluer, Ahmet; Mody, Sheila; Jain, Raksha; Dayton, Leigh Ann Bray; Godfrey, Emily M

Patient-Derived Intestinal Organoids in the Global Cystic Fibrosis Landscape

全球囊性纤维化领域中患者来源的肠道类器官

Kroes, Suzanne; Taylor-Cousar, Jennifer L; Zampoli, Marco; Karadag, Bülent; van der Ent, Cornelis K; de Winter-de Groot, Karin M; Beekman, Jeffrey M; Spelier, Sacha

Maximising opportunity for therapeutic success: sequential participation in cystic fibrosis nucleic acid-based therapy trials

最大限度提高治疗成功率:按顺序参与囊性纤维化核酸疗法试验

Mayer-Hamblett, Nicole; Kerper, Natanya R; Clancy, John P; Davies, Jane C; Taylor-Cousar, Jennifer L; Donaldson, Scott H; Bell, Scott C; Jain, Raksha; Simmonds, Nicholas J; Mall, Marcus A; Goss, Christopher H; Rayment, Jonathan H; Setiawan, Linda; Pilewski, Joseph M

Vanzacaftor-tezacaftor-deutivacaftor for children aged 6-11 years with cystic fibrosis (RIDGELINE Trial VX21-121-105): an analysis from a single-arm, phase 3 trial

Vanzacaftor-tezacaftor-deutivacaftor 用于治疗 6-11 岁囊性纤维化患儿(RIDGELINE 试验 VX21-121-105):一项单臂 3 期试验的分析

Hoppe, Jordana E; Kasi, Ajay S; Pittman, Jessica E; Jensen, Renee; Thia, Lena P; Robinson, Philip; Tirakitsoontorn, Pornchai; Ramsey, Bonnie; Mall, Marcus A; Taylor-Cousar, Jennifer L; McKone, Edward F; Tullis, Elizabeth; Salinas, Danieli B; Zhu, Jiaqiang; Chen, Yih-Chieh; Rodriguez-Romero, Violeta; Sosnay, Patrick R; Davies, Gwyneth

Vanzacaftor-tezacaftor-deutivacaftor versus elexacaftor-tezacaftor-ivacaftor in individuals with cystic fibrosis aged 12 years and older (SKYLINE Trials VX20-121-102 and VX20-121-103): results from two randomised, active-controlled, phase 3 trials

在12岁及以上囊性纤维化患者中,Vanzacaftor-tezacaftor-deutivacaftor 与 elexacaftor-tezacaftor-ivacaftor 的疗效比较(SKYLINE 试验 VX20-121-102 和 VX20-121-103):两项随机、活性对照、3期试验的结果

Keating, Claire; Yonker, Lael M; Vermeulen, François; Prais, Dario; Linnemann, Rachel W; Trimble, Aaron; Kotsimbos, Tom; Mermis, Joel; Braun, Andrew T; O'Carroll, Mark; Sutharsan, Sivagurunathan; Ramsey, Bonnie; Mall, Marcus A; Taylor-Cousar, Jennifer L; McKone, Edward F; Tullis, Elizabeth; Floreth, Tim; Michelson, Peter; Sosnay, Patrick R; Nair, Nitin; Zahigian, Rachel; Martin, Hannah; Ahluwalia, Neil; Lam, Anna; Horsley, Alexander

Abridging the 22-Item Sino-Nasal Outcome Test (SNOT-22) in People With Cystic Fibrosis: Limiting Survey Burden

简化囊性纤维化患者的22项鼻窦炎结局测试(SNOT-22):减轻调查负担

Chen, Haidee; Fischer, Jakob L; Tibbe, Tristan D; Sedaghat, Ahmad R; Han, Ethan J; Mace, Jess C; Alt, Jeremiah A; Bodner, Todd E; Chowdhury, Naweed I; Gao, Yuqing A; Hwang, Peter H; Khanwalkar, Ashoke; Kimple, Adam J; Lee, Jivianne T; Li, Douglas A; Norris, Meghan; Nayak, Jayakar V; Collins, Cameran; Patel, Zara M; Phillips, Katie; Poch, Katie; Schlosser, Rodney J; Smith, Kristine A; Soler, Zachary M; Suh, Jeffrey D; Turner, Grant A; Wang, Marilene B; Getz, Anne; Halderman, Ashleigh; Chung, Sei; Tervo, Jeremy P; Overdevest, Jonathan B; Cotter, Ryan A; Saavedra, Milene T; Taylor-Cousar, Jennifer L; Sim, Myung-Shin; Beswick, Daniel M

Transcriptomic and functional responses of the cystic fibrosis airway epithelium to CFTR modulator therapy

囊性纤维化气道上皮细胞对CFTR调节剂治疗的转录组和功能反应

Vladar, Eszter K; Gillen, Austin E; Yadav, Sangya; Murphree, Mikayla R; Baraghoshi, David; Harris, J Kirk; Pruesse, Elmar; Niemiec, Sierra S; Wilson, Alexandra Wm; Hisert, Katherine B; Humphries, Stephen M; Strand, Matthew; Lynch, David A; Seibold, Max A; Beswick, Daniel M; Taylor-Cousar, Jennifer L

Contraceptive use and pregnancy in cystic fibrosis: Survey findings from 10 cystic fibrosis centers

囊性纤维化患者的避孕措施和妊娠情况:来自10个囊性纤维化中心的调查结果

Godfrey, Emily M; Magaret, Amalia; Roe, Andrea; Taylor-Cousar, Jennifer L; Walker, Patricia; Langfelder-Schwind, Elinor; Kazmerski, Traci M; Jain, Raksha; Mody, Sheila K; Uluer, Ahmet; West, Natalie E; Bray, Leigh Ann; Hsu, Chialing; Fiastro, Anna; Stukovsky, Karen D Hinckley; Hadjiliadis, Dennis; Solomon, George M; Ladores-Barrett, Sigrid