AAV-delivered suppressor tRNA overcomes a nonsense mutation in mice
AAV 传递的抑制 tRNA 克服了小鼠的无义突变
期刊:Nature
影响因子:50.5
doi:10.1038/s41586-022-04533-3
Jiaming Wang #, Yue Zhang #, Craig A Mendonca #, Onur Yukselen, Khaja Muneeruddin, Lingzhi Ren, Jialing Liang, Chen Zhou, Jun Xie, Jia Li, Zhong Jiang, Alper Kucukural, Scott A Shaffer, Guangping Gao, Dan Wang