日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Regulated GATA1 expression as a universal gene therapy for Diamond-Blackfan anemia

调控GATA1表达作为治疗Diamond-Blackfan贫血症的通用基因疗法

Richard A Voit ,Xiaotian Liao ,Alexis Caulier ,Mateusz Antoszewski ,Blake Cohen ,Myriam Armant ,Henry Y Lu ,Travis J Fleming ,Elena Kamal ,Lara Wahlster ,Aoife M Roche ,John K Everett ,Angelina Petrichenko ,Mei-Mei Huang ,William Clarke ,Kasiani C Myers ,Craig Forester ,Antonio Perez-Atayde ,Frederic D Bushman ,Danilo Pellin ,Akiko Shimamura ,David A Williams ,Vijay G Sankaran