日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

In vivo site-specific engineering to reprogram T cells

利用体内位点特异性工程技术重编程T细胞

Nyberg, William A; Bernard, Pierre-Louis; Ngo, Wayne; Wang, Charlotte H; Ark, Jonathan; Rothrock, Allison; Borgo, Gina M; Kimmerly, Gabriella R; Jung, Jae Hyung; Allain, Vincent; Hamilton, Jennifer R; Baldwin, Alisha; Stickels, Robert; Wyman, Sarah; Khan, Safwaan H; Lang, Shanshan; Marsh, Donna; Almudhfar, Niran; Novick, Catherine; Mortazavi, Yasaman; Zhang, Shimin; AbdElwakil, Mahmoud M; Sandoval, Luis R; Hwang, Sidney; Chu, Simon N; Jung, Hyuncheol; Liu, Chang; Sharma, Devesh; McCreary, Travis; Li, Zhongmei; Satpathy, Ansuman T; Carnevale, Julia; Rutishauser, Rachel L; Cromer, M Kyle; Roybal, Kole T; Dodgson, Stacie E; Doudna, Jennifer A; Asokan, Aravind; Eyquem, Justin

Novel humanized loss-of-function NF1 mouse model of juvenile myelomonocytic leukemia.

新型人源化功能缺失型 NF1 小鼠幼年型骨髓单核细胞白血病模型。

Sinha Roshani, Patil Rachana Vinay, Romano Rosa, Sharma Devesh, Lee Esmond, Perriman Rhonda, Takeda Saori, Lesch Benjamin J, Yao Zhenyu, Liu Y Lucy, Cromer M Kyle, Porteus Matthew H, Bertaina Alice

Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells

组合碱基编辑技术将疾病矫正与造血干细胞和祖细胞的谱系扩增相结合

Jia, Kun; Soupene, Eric; Sinha, Roshani; Lesch, Benjamin J; Pendergast, Michael A; Choi, Rachel; Zhang, Xinyi; Foppiani, Elisabetta M; Kostamo, Zachary; Chu, Simon N; Sharma, Devesh; Yu, Xinjie; Cordero, Marco; Walters, Mark C; MacKenzie, Tippi C; Sheehan, Vivien A; Cromer, M Kyle

Mobilization meets antibody conditioning: A path toward safer engraftment

动员与抗体预处理相结合:通往更安全植入之路

Cromer, M Kyle

Highly efficient in vivo hematopoietic stem cell transduction using an optimized self-complementary adeno-associated virus

利用优化的自互补腺相关病毒实现高效的体内造血干细胞转导

Charlesworth, Carsten T; Homma, Shota; Amaya, Anais K; Dib, Carla; Vaidyanathan, Sriram; Tan, Tze-Kai; Miyauchi, Masashi; Nakauchi, Yusuke; Suchy, Fabian P; Wang, Sicong; Igarashi, Kyomi J; Cromer, M Kyle; Dudek, Amanda M; Amorin, Alvaro; Czechowicz, Agnieszka; Wilkinson, Adam C; Nakauchi, Hiromitsu

Protocol for efficient CRISPR/AAV-mediated genome editing and erythroid differentiation of human hematopoietic stem and progenitor cells.

利用 CRISPR/AAV 介导的基因组编辑和人类造血干细胞及祖细胞红系分化的有效方案

Sharma Devesh, Sinha Roshani, Lesch Benjamin J, Cromer M Kyle

In utero lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells.

子宫内脂质纳米颗粒递送可实现对造血干细胞的强效编辑

Worthington Atesh K, Borges Beltran, Lum Tony, Echeverri Elisa Schrader, Zada Fareha Moulana, Cordero Marco A, Kim Hyejin, Zenhausern Ryan, Celik Ozgenur, Shaw Cindy, Gutierrez-Martinez Paula, Omarova Marzhana, Blanchard Chris, Burns Sean, Cromer M Kyle, Dahlman James E, MacKenzie Tippi C

Enhancement of erythropoietic output by Cas9-mediated insertion of a natural variant in haematopoietic stem and progenitor cells.

通过 Cas9 介导将天然变异体插入造血干细胞和祖细胞,增强红细胞生成输出

Luna Sofia E, Camarena Joab, Hampton Jessica P, Majeti Kiran R, Charlesworth Carsten T, Soupene Eric, Selvaraj Sridhar, Jia Kun, Sheehan Vivien A, Cromer M Kyle, Porteus Matthew H

CRISPR nuclease off-target activity and mitigation strategies

CRISPR核酸酶脱靶活性及其缓解策略

Wienert, Beeke; Cromer, M Kyle

Identification of somatic mutations in parathyroid tumors using whole-exome sequencing

利用全外显子组测序鉴定甲状旁腺肿瘤中的体细胞突变

Cromer, M Kyle; Starker, Lee F; Choi, Murim; Udelsman, Robert; Nelson-Williams, Carol; Lifton, Richard P; Carling, Tobias