日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

High-efficiency base editing in the retina in primates and human tissues

灵长类动物和人类视网膜组织中的高效碱基编辑

Muller, Alissa; Sullivan, Jack; Schwarzer, Wibke; Wang, Mantian; Park-Windhol, Cindy; Hasler, Pascal W; Janeschitz-Kriegl, Lucas; Duman, Mert; Klingler, Beryll; Matsell, Jane; Hostettler, Simon Manuel; Galliker, Patricia; Hou, Yanyan; Balmer, Pierre; Virág, Tamás; Barrera, Luis Alberto; Young, Lauren; Xu, Quan; Magda, Dániel Péter; Kilin, Ferenc; Khadka, Arogya; Moreau, Pierre-Henri; Fellmann, Lyne; Azoulay, Thierry; Quinodoz, Mathieu; Karademir, Duygu; Leppert, Juna; Fratzl, Alex; Kosche, Georg; Sharma, Ruchi; Montford, Jair; Cattaneo, Marco; Croyal, Mikaël; Cronin, Therese; Picelli, Simone; Grison, Alice; Cowan, Cameron S; Kusnyerik, Ákos; Anders, Philipp; Renner, Magdalena; Nagy, Zoltán Zsolt; Szabó, Arnold; Bharti, Kapil; Rivolta, Carlo; Scholl, Hendrik P N; Bryson, David; Ciaramella, Giuseppe; Roska, Botond; György, Bence

The ambition for a one-and-done vision-saving AAV vector

目标是研发一种一次性挽救视力的AAV载体

Cronin, Therese

Generation of a compound heterozygous ABCA4 rat model with pathological features of STGD1.

构建具有 STGD1 病理特征的复合杂合子 ABCA4 大鼠模型

Morival Clément, Croyal Mikaël, Remy Séverine, Mortier Elodie, Libeau Lyse, Veziers Joëlle, Provost Nathalie, Demilly Joanna, Mendes-Madeira Alexandra, Isiegas Carolina, Tesson Laurent, Anegon Ignacio, Adjali Oumeya, Cronin Therese

Intravitreal air tamponade after AAV2 subretinal injection modifies retinal EGFP distribution

AAV2视网膜下注射后进行玻璃体内空气填充可改变视网膜EGFP分布。

Ducloyer, Jean-Baptiste; Pichard, Virginie; Mevel, Mathieu; Galy, Anne; Lefevre, Gaelle M; Brument, Nicole; Alvarez-Dorta, Dimitri; Deniaud, David; Mendes-Madeira, Alexandra; Libeau, Lyse; Le Guiner, Caroline; Cronin, Therese; Adjali, Oumeya; Weber, Michel; Le Meur, Guylène

Risk Mitigation of Immunogenicity: A Key to Personalized Retinal Gene Therapy

降低免疫原性风险:实现个性化视网膜基因治疗的关键

Varin, Juliette; Morival, Clément; Maillard, Noémien; Adjali, Oumeya; Cronin, Therese