日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Author Correction: Intrathecal onasemnogene abeparvovec for treatment-experienced patients with spinal muscular atrophy: a phase 3b, open-label trial

作者更正:鞘内注射onasemnogene abeparvovec治疗既往接受过治疗的脊髓性肌萎缩症患者:一项3b期开放标签试验

Kwon, Jennifer M; Munell, Francina; Le Goff, Laure; Yuge, Kotaro; Kato, Tamaki; Cances, Claude; De Waele, Liesbeth; Woodcock, Ian R; Mercuri, Eugenio M; Proud, Crystal M; Darras, Basil T; Hayes, Leslie H; Oskoui, Maryam; Visootsak, Jeannie; Williams, Gemma; Ilić, Andreja; Yang, Lina; van der Pol, W Ludo

Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial

鞘内注射onasemnogene abeparvovec治疗初治脊髓性肌萎缩症患者:一项3期随机对照试验

Proud, Crystal M; Vũ, Dũng Chí; Wilmshurst, Jo M; Sanmaneechai, Oranee; Gulati, Sheffali; Xiong, Hui; Moreno, Hugo C; Tay, Stacey Kiat Hong; Thong, Meow-Keong; Born, Alfred Peter; Banzzatto Ortega, Adriana; Jong, Yuh-Jyh; Al-Muhaizea, Mohammad A; Lee, Anna W; Visootsak, Jeannie; Tauscher-Wisniewski, Sitra; Alecu, Iulian; Parlikar, Rutvick; Finkel, Richard S

Bidirectional CRISPR screens decode a GLIS3-dependent fibrotic cell circuit.

双向 CRISPR 筛选解码 GLIS3 依赖性纤维化细胞回路。

Pokatayev Vladislav, Jaiswal Alok, Shih Angela R, Segerstolpe à sa, Li Bihua, Creasey Elizabeth A, Zhao Yanhua, Lin Crystal, Murphy Shane, Chou Chih-Hung, Graham Daniel B, Xavier Ramnik J

Reciprocal regulation of fibroblast-macrophage equilibrium governs skin integrity.

成纤维细胞与巨噬细胞平衡的相互调节决定着皮肤的完整性。

Vollmers Apple Cortez, Wu Sunny Z, Altieri Anthony, McCartney Erika E, Bender Hannah, Davidson Christopher D, Lee Wyne P, Zhang Juan, Hu Crystal, Jeet Surinder, Hall Ben, Irizarry-Caro Ricardo A, Guarnieri Alberto, Santosa Endi K, Preston Jessica, Uttarwar Salil, Vander Heiden Jason A, Chung Yein, Ortiz Willie, Long Michael, Asuncion Raymond, Yang Yeqing Angela, Jiang Jean X, Modrusan Zora, Chintalacharuvu Subba, Moussion Christine, Krishnamurty Akshay T, Fu Wenxian, Müller Sören, Buechler Matthew B, Turley Shannon J

Commensal-derived trehalose monocorynomycolate triggers γδ T cell-driven protective ocular barrier immunity.

共生菌来源的海藻糖单丝氨酸酯可触发 α1T 细胞驱动的保护性眼屏障免疫。

Xu Xiaoyan, Rigas Yannis E, Mattapallil Mary J, Guo Jing, Sakamoto Keiko, Nagao Keisuke, Nagarajan Vijayaraj, Bohrnsen Eric, Richards Crystal, Gupta Akriti, Gaud Guillaume, Love Paul E, Jiang Timothy, Zhang Amy, Xu Biying, Peng Zixuan, Jittayasothorn Yingyos, Carr Mary A, Magone M Teresa, Brandes Nathan T, Shane Jackie, Schwarz Benjamin, St Leger Anthony J, Caspi Rachel R

Self-Propagating Nature of Pathogenic Extracellular Vesicles Associated with Smoking and COPD

吸烟和慢性阻塞性肺病相关的致病性细胞外囊泡的自我增殖特性

Margaroli, Camilla; Genschmer, Kristopher R; Xu, Ningyong; Lewis, Crystal; Smith, Julian B; Stacks, Delores A; Sari, Ezgi; Wilson, Landon; Blagburn, Kyli; Richter, Robert P; Viera, Liliana; Guo, Yuanyuan; Finley, Dakota; Madison, Matthew C; Gaggar, Amit; Blalock, James E

Human Rabies Deaths - Minnesota and California, 2024

2024年明尼苏达州和加利福尼亚州人类狂犬病死亡人数

Ireland, Malia; Fritz, Curtis L; Holzbauer, Stacy; Klumb, Carrie; Bye, Maria; Bauck, Leah; Bakken, Amanda; Dethloff, Michelle; Campagna, Rebecca; Deldari, Mojgan; Hepp, Susan; Lopez, Ruth; Messenger, Sharon; Preas, Christopher; Rendon, Aimee; Koch-Kumar, Stephanie; Rangel, Maria; Bains, Kanwaldeep; Bulawit, Jeffrey; Al Saghbini, Samer; Solis, Trinidad; Prado, Joe; Zweifler, John; Berber, Leticia; Vohra, Rais; Santana, Ignacio A; Sandoval, Salvador; Sahota, Parmjit; Hendrickson, Mark; Black, Megan; Chavez, Gloria; Schwab, Andrew; Yager, Pamela A; Niezgoda, Michael; Wicker, Vaughn V; Gigante, Crystal M; Orciari, Lillian A; Blanton, Jesse D; Bonaparte, Sarah C; Earnest, Rebecca; Wallace, Ryan M

Imported Human Rabies - Kentucky and Ohio, 2024

2024年肯塔基州和俄亥俄州输入性人类狂犬病病例

Barger, Alexandra; Margrey, Sara F; Siu, Allison W; Wallace, Ryan; Earnest, Rebecca; Frankel, Molly; Eshete, Hermella; Swisshelm, Carolyn; Shiltz, Eli; Wright, Kimberly; Allen, Arminda; Orciari, Lillian A; Gigante, Crystal M; Condori, Rene; Yager, Pamela; Niezgoda, Michael; Satheshkumar, Panayampalli S; Thoroughman, Douglas; Winter, Kathleen; Giesbrecht, Kelly

Antipsychotic Medication Use by Older Adults

老年人使用抗精神病药物的情况

Olfson, Mark; Xie, Fangzhou; Bushnell, Greta; Hua, Jialiang; Miles, Jennifer; Crystal, Stephen