日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial

对侧眼注射AAV2基因疗法治疗RPE65基因突变引起的儿童期发病失明患者的安全性和疗效持久性:一项后续1期试验

Bennett, Jean; Wellman, Jennifer; Marshall, Kathleen A; McCague, Sarah; Ashtari, Manzar; DiStefano-Pappas, Julie; Elci, Okan U; Chung, Daniel C; Sun, Junwei; Wright, J Fraser; Cross, Dominique R; Aravand, Puya; Cyckowski, Laura L; Bennicelli, Jeannette L; Mingozzi, Federico; Auricchio, Alberto; Pierce, Eric A; Ruggiero, Jason; Leroy, Bart P; Simonelli, Francesca; High, Katherine A; Maguire, Albert M

Plasticity of the human visual system after retinal gene therapy in patients with Leber's congenital amaurosis

莱伯氏先天性黑蒙患者接受视网膜基因治疗后,人类视觉系统的可塑性

Ashtari, Manzar; Zhang, Hui; Cook, Philip A; Cyckowski, Laura L; Shindler, Kenneth S; Marshall, Kathleen A; Aravand, Puya; Vossough, Arastoo; Gee, James C; Maguire, Albert M; Baker, Chris I; Bennett, Jean

AAV2 gene therapy readministration in three adults with congenital blindness

对三名患有先天性失明的成年人进行AAV2基因治疗的再次给药

Bennett, Jean; Ashtari, Manzar; Wellman, Jennifer; Marshall, Kathleen A; Cyckowski, Laura L; Chung, Daniel C; McCague, Sarah; Pierce, Eric A; Chen, Yifeng; Bennicelli, Jeannette L; Zhu, Xiaosong; Ying, Gui-Shuang; Sun, Junwei; Wright, J Fraser; Auricchio, Alberto; Simonelli, Francesca; Shindler, Kenneth S; Mingozzi, Federico; High, Katherine A; Maguire, Albert M

The human visual cortex responds to gene therapy-mediated recovery of retinal function

人类视觉皮层对基因治疗介导的视网膜功能恢复有反应

Ashtari, Manzar; Cyckowski, Laura L; Monroe, Justin F; Marshall, Kathleen A; Chung, Daniel C; Auricchio, Alberto; Simonelli, Francesca; Leroy, Bart P; Maguire, Albert M; Shindler, Kenneth S; Bennett, Jean

Medial temporal structures and memory functions in adolescents with heavy cannabis use

青少年大量吸食大麻对其内侧颞叶结构和记忆功能的影响

Ashtari, Manzar; Avants, Brian; Cyckowski, Laura; Cervellione, Kelly L; Roofeh, David; Cook, Philip; Gee, James; Sevy, Serge; Kumra, Sanjiv

Response to Wang et al

对 Wang 等人的回应

Watkins, Stephanie K; Zhu, Ziqiang; Riboldi, Elena; Shafer-Weaver, Kim A; Stagliano, Katherine ER; Sklavos, Martha M; Ambs, Stefan; Yagita, Hideo; Hurwitz, Arthur A; Merovci, Aurora; Solis-Herrera, Carolina; Daniele, Giuseppe; Eldor, Roy; Fiorentino, Teresa Vanessa; Tripathy, Devjit; Xiong, Juan; Perez, Zandra; Norton, Luke; Abdul-Ghani, Muhammad A; DeFronzo, Ralph A; Cairns, Dana M; Pignolo, Robert J; Uchimura, Tomoya; Brennan, Tracy A; Lindborg, Carter M; Xu, Meiqi; Kaplan, Frederick S; Shore, Eileen M; Zeng, Li; Zhou, Yan; Gormley, Matthew J; Hunkapiller, Nathan M; Kapidzic, Mirhan; Stolyarov, Yana; Feng, Victoria; Nishida, Masakazu; Drake, Penelope M; Bianco, Katherine; Wang, Fei; McMaster, Michael T; Fisher, Susan J; Knight, Deborah A; Ngiow, Shin Foong; Li, Ming; Parmenter, Tiffany; Mok, Stephen; Cass, Ashley; Haynes, Nicole M; Kinross, Kathryn; Yagita, Hideo; Koya, Richard C; Graeber, Thomas G; Ribas, Antoni; McArthur, Grant A; Smyth, Mark J; Luo, Min; Guan, Xiaoqun; Luczak, Elizabeth D; Lang, Di; Kutschke, William; Gao, Zhan; Yang, Jinying; Glynn, Patric; Sossalla, Samuel; Swaminathan, Paari D; Weiss, Robert M; Yang, Baoli; Rokita, Adam G; Maier, Lars S; Efimov, Igor R; Hund, Thomas J; Anderson, Mark E; Mareninova, Olga A; Hermann, Kip; French, Samuel W; O’Konski, Mark S; Pandol, Stephen J; Webster, Paul; Erickson, Ann H; Katunuma, Nobuhiko; Gorelick, Fred S; Gukovsky, Ilya; Gukovskaya, Anna S; Agnihotri, Sameer; Gajadhar, Aaron S; Ternamian, Christian; Gorlia, Thierry; Diefes, Kristin L; Mischel, Paul S; Kelly, Joanna; McGown, Gail; Thorncroft, Mary; Carlson, Brett L; Sarkaria, Jann N; Margison, Geoffrey P; Aldape, Kenneth; Hawkins, Cynthia; Hegi, Monika; Guha, Abhijit; Ashtari, Manzar; Cyckowski, Laura L; Monroe, Justin F; Marshall, Kathleen A; Chung, Daniel C; Auricchio, Alberto; Simonelli, Francesca; Leroy, Bart P; Maguire, Albert M; Shindler, Kenneth S; Bennett, Jean; Zhang, Denghong; Contu, Riccardo; Latronico, Michael VG; Zhang, Jianlin; Rizzi, Roberto; Catalucci, Daniele; Miyamoto, Shigeki; Huang, Katherine; Ceci, Marcello; Gu, Yusu; Dalton, Nancy D; Peterson, Kirk L; Guan, Kun-Liang; Brown, Joan Heller; Chen, Ju; Sonenberg, Nahum; Condorelli, Gianluigi; Mandinova, Anna; Kolev, Vihren; Neel, Victor; Hu, Bing; Stonely, Wesley; Lieb, Jocelyn; Wu, Xunwei; Colli, Claudia; Han, Rong; Pazin, Michael J; Ostano, Paola; Dummer, Reinhard; Brissette, Janice L; Dotto, G Paolo; Adler, David H; Cogan, Joy D; Phillips, John A III; Schnetz-Boutaud, Nathalie; Milne, Ginger L; Iverson, Tina; Stein, Jeffrey A; Brenner, David A; Morrow, Jason D; Boutaud, Olivier; Oates, John A; Wang, Yanfeng; Litvinov, Rustem I; Chen, Xinsheng; Bach, Tami L; Lian, Lurong; Petrich, Brian G; Monkley, Susan J; Kanaho, Yasunori; Critchley, David R; Sasaki, Takehiko; Birnbaum, Morris J; Weisel, John W; Hartwig, John; Abrams, Charles S; Farese, Robert V; Sajan, Mini P; Yang, Hong; Li, Pengfei; Mastorides, Steven; Gower, William R Jr; Nimal, Sonali; Choi, Cheol Soo; Kim, Sheene; Shulman, Gerald I; Kahn, C Ronald; Braun, Ursula; Leitges, Michael; Kim, Ellen J; Hess, Stephen; Richardson, Stephen K; Newton, Sara; Showe, Louise C; Benoit, Bernice M; Ubriani, Ravi; Vittorio, Carmela C; Junkins-Hopkins, Jacqueline M; Wysocka, Maria; Rook, Alain H; Vukmanovic-Stejic, Milica; Zhang, Yan; Cook, Joanne E; Fletcher, Jean M; McQuaid, Arthur; Masters, Joanne E; Rustin, Malcolm HA; Taams, Leonie S; Beverley, Peter CL; Macallan, Derek C; Akbar, Arne N; Puglielli, Luigi; Friedlich, Avi L; Setchell, Kenneth DR; Nagano, Seiichi; Opazo, Carlos; Cherny, Robert A; Barnham, Kevin J; Wade, John D; Melov, Simon; Kovacs, Dora M; Bush, Ashley I; Vukmanovic-Stejic, Milica; Zhang, Yan; Cook, Joanne E; Fletcher, Jean M; McQuaid, Arthur; Masters, Joanne E; Rustin, Malcolm HA; Taams, Leonie S; Beverley, Peter CL; Macallan, Derek C; Akbar, Arne N; Altshuler, David; Hirschhorn, Joel N