Fully Human Bifunctional Intrabodies Achieve Graded Reduction of Intracellular Tau and Rescue Survival of MAPT Mutation iPSC-derived Neurons
全人源双功能胞内抗体可逐步降低细胞内Tau蛋白水平并挽救MAPT突变iPSC衍生神经元的存活率
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doi:10.1101/2024.05.28.596248
D'Brant, Lianna; Rugenstein, Natasha; Na, Su Kyoung; Miller, Michael J; Czajka, Timothy F; Trudeau, Nicole; Fitz, Emily; Tomaszek, Lindsay; Fisher, Elizabeth S; Mash, Ethan; Joy, Shona; Lotz, Steven; Borden, Susan; Stevens, Katherine; Goderie, Susan K; Wang, Yue; Bertucci, Taylor; Karch, Celeste M; Temple, Sally; Butler, David C