Design considerations for C9orf72 disease prevention trials
C9orf72疾病预防试验的设计考虑因素
期刊:Brain
影响因子:11.7
doi:10.1093/brain/awaf290
Benatar, Michael; Staffaroni, Adam M; Wuu, Joanne; McDermott, Michael P; Quintana, Melanie; Swidler, Jean; Andersen, Gail; Huey, Edward D; Turner, Martin R; Macklin, Eric A; Berry, James D; McMillan, Corey T; Gendron, Tania; Onyike, Chiadi; Rosen, Howard; Heuer, Hilary W; Grignon, Anne-Laure; Dave, Kuldip D; Balas, Calaneet; Gleixner, Amanda; Satlin, Andrew; Dunn, Billy; Dacks, Penny; Boxer, Adam L