日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Interindividual variability in immune response to AAV ocular gene delivery across species impedes immunomonitoring

不同物种对AAV眼部基因递送的免疫反应存在个体差异,这阻碍了免疫监测。

Ren, Duohao; Chauveau, Gaelle A; Vendomele, Julie; Cabon, Emilie; Pineiro, Audrey; Vignal-Clermont, Catherine; Saliba, Hanadi; Ronzitti, Giuseppe; Galy, Anne; Dalkara, Deniz; Pulman, Juliette; Ail, Divya; Fisson, Sylvain

Retinal organoids mirror CRISPR-Cas9 gene editing efficiency observed in vivo

视网膜类器官反映了体内观察到的 CRISPR-Cas9 基因编辑效率。

Pulman, Juliette; Malki, Hugo; Oudin, Paul; Aydin, Ecem; Tran, Sophie; Visticot, Laura; Robert, Camille; De Cian, Anne; As, Marie; Goureau, Olivier; Concordet, Jean-Paul; Dalkara, Deniz

Impact of DNase digestion on titer measurements of engineered adeno-associated virus serotypes.

DNase 消化对工程化腺相关病毒血清型滴度测定的影响

Zin Emilia A, Desrosiers Melissa, Ocari Tommaso, Labernede Guillaume, Robert Camille, Izabella Charlotte, Saubamea Bruno, Ferrari Ulisse, Dalkara Deniz

Reactivating the phototransduction cascade with a mutation agnostic gene therapy preserves vision in rod-cone dystrophies

利用不依赖特定基因突变的基因疗法重新激活光转导级联反应,可以保护视杆细胞-视锥细胞营养不良患者的视力。

Simon, Cardillia-Joe; Khabou, Hanen; Chaffiol, Antoine; Rucli, Marco; Finzi, Marion; Norberg, Nat; Grimaud, Anaïs; Mücher, Brix; Desrosiers, Mélissa; Sancho, Serge; Bonilha, Vera Lucia; Grieve, Kate; Duebel, Jens; Paques, Michel; Picaud, Serge; Sahel, José Alain; Audo, Isabelle; Herlitze, Stefan; Dalkara, Deniz

Photoactivated adenylyl cyclase in cortical astrocytes promotes synaptic potentiation and reveals alterations in Huntington's disease.

皮质星形胶质细胞中的光激活腺苷酸环化酶促进突触增强,并揭示亨廷顿病中的改变。

Sitjà-Roqueta Laia, Ngum Neville M, Zherebtsov Evgenii A, Küçükerden Melike, Givehchi Maryam, Bova Valentina, Delicata Francis, Anaya-Cubero Elena, Santamaria Enrique, Fernández-Irigoyen Joaquín, Conde-Berriozabal Sara, Castañé Anna, Sokolovski Sergei, Rafailov Edik, Rodríguez Manuel J, Alberch Jordi, Dalkara Deniz, Möglich Andreas, Bykov Alexander, Meglinski Igor, Parri H Rheinallt, Masana Mercè

Characterization of anti-AAV2 neutralizing antibody levels in sheep prior to and following intravitreal AAV2.7m8 injection

对绵羊玻璃体内注射 AAV2.7m8 前后抗 AAV2 中和抗体水平进行表征

Ross, Maya; Sade, Kareen; Obolensky, Alexey; Averbukh, Edward; Desrosiers, Melissa; Rosov, Alexander; Dvir, Hay; Gootwine, Elisha; Banin, Eyal; Dalkara, Deniz; Ofri, Ron

ACIDES: on-line monitoring of forward genetic screens for protein engineering

ACIDES:用于蛋白质工程的正向基因筛选的在线监测

Nemoto, Takahiro; Ocari, Tommaso; Planul, Arthur; Tekinsoy, Muge; Zin, Emilia A; Dalkara, Deniz; Ferrari, Ulisse

Gene augmentation in FAM161A ciliopathy: Toward functional vision rescue

FAM161A纤毛病中的基因增强:迈向功能性视力恢复

Sahel, José-Alain; Marazova, Katia; Dalkara, Deniz

Developing New Vectors for Retinal Gene Therapy

开发用于视网膜基因治疗的新型载体

Zin, Emilia A; Ozturk, Bilge E; Dalkara, Deniz; Byrne, Leah C

Adeno-Associated Virus (AAV) - Based Gene Therapies for Retinal Diseases: Where are We?

基于腺相关病毒 (AAV) 的视网膜疾病基因疗法:我们目前处于什么阶段?

Ail, Divya; Malki, Hugo; Zin, Emilia A; Dalkara, Deniz