Amelioration of metabolic and behavioral defects through base editing in the Pah(R408W) phenylketonuria mouse model
通过碱基编辑改善 Pah(R408W) 苯丙酮尿症小鼠模型的代谢和行为缺陷
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.11.032
Yin, Shuming; Gao, Liangcai; Sun, Xiaoyue; Zhang, Mei; Gao, Hongyi; Chen, Xiaoqing; Zhang, Dan; Ming, Xinyu; Yang, Lei; Hu, Yaqiang; Chen, Xi; Liu, Meizhen; Zhan, Xia; Guan, Yuting; Wang, Liren; Han, Lianshu; Zhu, Ping; Li, Dali