Intraparenchymal convection enhanced delivery of AAV in sheep to treat Mucopolysaccharidosis IIIC
绵羊实质内对流增强 AAV 输送治疗粘多糖贮积症 IIIC
期刊:Journal of Translational Medicine
影响因子:6.1
doi:10.1186/s12967-023-04208-1
Claire O'Leary, Gabriella Forte, Nadia L Mitchell, Amir Saam Youshani, Adam Dyer, Martin P Wellby, Katharina N Russell, Samantha J Murray, Nelly Jolinon, Simon A Jones, Kevin Stacey, Daniel M Davis, Els Henckaerts, David N Palmer, Ian Kamaly-Asl, Brian W Bigger