A transcriptomics-based drug repositioning approach to identify drugs with similar activities for the treatment of muscle pathologies in spinal muscular atrophy (SMA) models
基于转录组学的药物重新定位方法,用于识别具有类似活性的药物,用于治疗脊髓性肌萎缩 (SMA) 模型中的肌肉病变
期刊:Human Molecular Genetics
影响因子:3.1
doi:10.1093/hmg/ddad192
Joseph M Hoolachan, Eve McCallion, Emma R Sutton, Özge Çetin, Paloma Pacheco-Torres, Maria Dimitriadi, Suat Sari, Gavin J Miller, Magnus Okoh, Lisa M Walter, Peter Claus, Matthew J A Wood, Daniel P Tonge, Melissa Bowerman