Lysosomal and network alterations in human mucopolysaccharidosis type VII iPSC-derived neurons
人类粘多糖贮积症 VII 型 iPSC 衍生神经元中的溶酶体和网络改变
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-018-34523-3
Neus Bayó-Puxan, Ana Paula Terrasso, Sophie Creyssels, Daniel Simão, Christina Begon-Pescia, Marina Lavigne, Sara Salinas, Florence Bernex, Assumpció Bosch, Vasiliki Kalatzis, Thierry Levade, Ana Maria Cuervo, Philippe Lory, Antonella Consiglio, Catarina Brito, Eric J Kremer