日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Large-scale drug screening in iPSC-derived motor neurons from sporadic ALS patients identifies a potential combinatorial therapy

对散发性ALS患者诱导多能干细胞衍生的运动神经元进行大规模药物筛选,发现了一种潜在的联合疗法

Bye, Christopher R; Qian, Elizabeth; Lim, Katherine; Daniszewski, Maciej; Garton, Fleur C; Trần-Lê, Bảo C; Liang, Helena H; Lin, Tian; Lock, John G; Crombie, Duncan E; Morgan, Steven; Hu, Yi; Barton, Samantha K; Palmer, Lucy M; Djouma, Elvan; Kodikara, Saritha; Lê Cao, Kim-Anh; Dharmadasa, Thanuja; Henders, Anjali K; Ziser, Laura A; Kiernan, Matthew C; Talbot, Kevin; Needham, Merrilee; Fletcher, Susan; Talman, Paul; Mathers, Susan; Wray, Naomi R; Hewitt, Alex W; Pebay, Alice; Turner, Bradley J

Driving Hydrolysis and Acetolysis of Poly(ethylene terephthalate) (PET) by Microwave and Thermal Energy Inputs: A Comparative Study

利用微波和热能驱动聚对苯二甲酸乙二醇酯(PET)水解和乙酰化:一项比较研究

Pereira, Patrícia; Daniszewski, Ashley C; Staack, Matthew; Salmanzadeh, Emir; Toraman, Hilal Ezgi; Hu, Jianli; Pester, Christian W; Savage, Phillip E

Human pluripotent stem cell-derived retinal ganglion cells: advances in differentiation and translational applications

人类多能干细胞衍生的视网膜神经节细胞:分化和转化应用方面的进展

Ma, Jessica Yuen Wuen; Daniszewski, Maciej; Pébay, Alice

A semi-automated pipeline for quantifying drusen-like deposits in human induced pluripotent stem cell-derived retinal pigment epithelium cells

用于量化人类诱导性多能干细胞来源的视网膜色素上皮细胞中视网膜黄斑硬化症样沉积物的半自动化流程

Jenna Hall, Maciej Daniszewski, Shane Cheung, Kalyan Shobhana, Himeesh Kumar, Helena H Liang, Henry Beetham, Ellie Cho, Carla Abbott, Alex W Hewitt, Kaylene J Simpson, Robyn H Guymer, Daniel Paull, Alice Pébay, Grace E Lidgerwood

Generation of a gene-corrected human isogenic iPSC line from an Alzheimer's disease iPSC line carrying the PSEN1 H163R mutation.

从携带 PSEN1 H163R 突变的阿尔茨海默病 iPSC 系中生成基因校正的人类同源 iPSC 系

Hernández Damián, Morgan Schlicht Stephanie, Elli Clarke Jordan, Daniszewski Maciej, Karch Celeste M, Goate Alison M, Pébay Alice

A village in a dish model system for population-scale hiPSC studies

用于群体规模hiPSC研究的“培养皿中的村庄”模型系统

Drew R Neavin ,Angela M Steinmann # ,Nona Farbehi # ,Han Sheng Chiu # ,Maciej S Daniszewski # ,Himanshi Arora ,Yasmin Bermudez ,Cátia Moutinho ,Chia-Ling Chan ,Monique Bax ,Mubarika Tyebally ,Vikkitharan Gnanasambandapillai ,Chuan E Lam ,Uyen Nguyen ,Damián Hernández ,Grace E Lidgerwood ,Robert M Graham ,Alex W Hewitt ,Alice Pébay ,Nathan J Palpant ,Joseph E Powell

AAV capsid bioengineering in primary human retina models

人类视网膜原代模型中的 AAV 衣壳生物工程

Adrian Westhaus, Steven S Eamegdool, Milan Fernando, Paula Fuller-Carter, Alicia A Brunet, Annie L Miller, Rabab Rashwan, Maddison Knight, Maciej Daniszewski, Grace E Lidgerwood, Alice Pébay, Alex Hewitt, Giorgia Santilli, Adrian J Thrasher, Livia S Carvalho, Anai Gonzalez-Cordero, Robyn V Jamieson,

Transcriptomic and proteomic retinal pigment epithelium signatures of age-related macular degeneration

年龄相关性黄斑变性的转录组学和蛋白质组学视网膜色素上皮特征

Anne Senabouth #, Maciej Daniszewski #, Grace E Lidgerwood #, Helena H Liang, Damián Hernández, Mehdi Mirzaei, Stacey N Keenan, Ran Zhang, Xikun Han, Drew Neavin, Louise Rooney, Maria Isabel G Lopez Sanchez, Lerna Gulluyan, Joao A Paulo, Linda Clarke, Lisa S Kearns, Vikkitharan Gnanasambandapillai, 

Retinal ganglion cell-specific genetic regulation in primary open-angle glaucoma

原发性开角型青光眼的视网膜神经节细胞特异性基因调控

Maciej Daniszewski, Anne Senabouth, Helena H Liang, Xikun Han, Grace E Lidgerwood, Damián Hernández, Priyadharshini Sivakumaran, Jordan E Clarke, Shiang Y Lim, Jarmon G Lees, Louise Rooney, Lerna Gulluyan, Emmanuelle Souzeau, Stuart L Graham, Chia-Ling Chan, Uyen Nguyen, Nona Farbehi, Vikkitharan Gn

AAV2-mediated gene therapy for Bietti crystalline dystrophy provides functional CYP4V2 in multiple relevant cell models

AAV2 介导的 Bietti 结晶性营养不良症基因治疗可在多种相关细胞模型中提供功能性 CYP4V2

Jiang-Hui Wang, Grace E Lidgerwood, Maciej Daniszewski, Monica L Hu, Georgina E Roberts, Raymond C B Wong, Sandy S C Hung, Michelle E McClements, Alex W Hewitt, Alice Pébay, Doron G Hickey, Thomas L Edwards