日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A pothole-filling strategy for selective targeting of rCUG-repeats associated with myotonic dystrophy type 1

一种针对与1型强直性肌营养不良症相关的rCUG重复序列的选择性靶向治疗策略

Perera, J Dinithi R; Thadke, Shivaji A; Thrikawala, Savani W; Dhami, Isha; Hridya, V M; Mukherjee, Arnab; Paul, Ananya; Wilson, W David; Tan, Keith W R; Chan, Nicholas Z W; Phan, Anh Tuân; Ly, Danith H

Self-Avoiding Gamma Peptide Nucleic Acids for Selective Targeting of RNA Secondary Structures

用于选择性靶向RNA二级结构的自回避γ肽核酸

Dhami, Isha; Thadke, Shivaji A; Perera, J Dinithi R; Batwal, Ramesh; Zheng, En; Thrikawala, Savani W; Aryal, Babita; Ly, Danith H

Synthesis of Janus Bases for Targeting C‑G and U-U Pairs of CUG-RNA Repeats Associated with Myotonic Dystrophy Type 1

合成 Janus 碱基以靶向与 1 型强直性肌营养不良症相关的 CUG-RNA 重复序列中的 C-G 和 UU 对

Thadke, Shivaji A; Perera, J Dinithi R; Thrikawala, Savani W; Ly, Danith H

The NIH Somatic Cell Genome Editing program

美国国立卫生研究院体细胞基因组编辑计划

Saha, Krishanu; Sontheimer, Erik J; Brooks, P J; Dwinell, Melinda R; Gersbach, Charles A; Liu, David R; Murray, Stephen A; Tsai, Shengdar Q; Wilson, Ross C; Anderson, Daniel G; Asokan, Aravind; Banfield, Jillian F; Bankiewicz, Krystof S; Bao, Gang; Bulte, Jeff W M; Bursac, Nenad; Campbell, Jarryd M; Carlson, Daniel F; Chaikof, Elliot L; Chen, Zheng-Yi; Cheng, R Holland; Clark, Karl J; Curiel, David T; Dahlman, James E; Deverman, Benjamin E; Dickinson, Mary E; Doudna, Jennifer A; Ekker, Stephen C; Emborg, Marina E; Feng, Guoping; Freedman, Benjamin S; Gamm, David M; Gao, Guangping; Ghiran, Ionita C; Glazer, Peter M; Gong, Shaoqin; Heaney, Jason D; Hennebold, Jon D; Hinson, John T; Khvorova, Anastasia; Kiani, Samira; Lagor, William R; Lam, Kit S; Leong, Kam W; Levine, Jon E; Lewis, Jennifer A; Lutz, Cathleen M; Ly, Danith H; Maragh, Samantha; McCray, Paul B Jr; McDevitt, Todd C; Mirochnitchenko, Oleg; Morizane, Ryuji; Murthy, Niren; Prather, Randall S; Ronald, John A; Roy, Subhojit; Roy, Sushmita; Sabbisetti, Venkata; Saltzman, W Mark; Santangelo, Philip J; Segal, David J; Shimoyama, Mary; Skala, Melissa C; Tarantal, Alice F; Tilton, John C; Truskey, George A; Vandsburger, Moriel; Watts, Jonathan K; Wells, Kevin D; Wolfe, Scot A; Xu, Qiaobing; Xue, Wen; Yi, Guohua; Zhou, Jiangbing

Publisher Correction: Shape selective bifacial recognition of double helical DNA

出版商更正:双螺旋DNA的形状选择性双面识别

Goren, Talia; Vashdi, Dana R; Beeri, Itai; Thadke, Shivaji A; Hridya, V M; Perera, J Dinithi R; Gil, Roberto R; Mukherjee, Arnab; Ly, Danith H

Bifunctional small molecule-oligonucleotide hybrid as microRNA inhibitor

双功能小分子-寡核苷酸杂合物作为microRNA抑制剂

Bhattarai, Umesh; Hsieh, Wei-Che; Yan, Hao; Guo, Zhi-Fo; Shaikh, Ashif Yasin; Soltani, Aria; Song, Yabin; Ly, Danith H; Liang, Fu-Sen

In utero nanoparticle delivery for site-specific genome editing

利用纳米颗粒在子宫内进行位点特异性基因组编辑

Ricciardi, Adele S; Bahal, Raman; Farrelly, James S; Quijano, Elias; Bianchi, Anthony H; Luks, Valerie L; Putman, Rachael; López-Giráldez, Francesc; Coşkun, Süleyman; Song, Eric; Liu, Yanfeng; Hsieh, Wei-Che; Ly, Danith H; Stitelman, David H; Glazer, Peter M; Saltzman, W Mark

Shape selective bifacial recognition of double helical DNA

双螺旋DNA的形状选择性双面识别

Thadke, Shivaji A; Hridya, V M; Perera, J Dinithi R; Gil, Roberto R; Mukherjee, Arnab; Ly, Danith H

RNA-Templated Concatenation of Triplet Nucleic-Acid Probe

RNA模板化的三联核酸探针串联

Bahal, Raman; Manna, Arunava; Hsieh, Wei-Che; Thadke, Shivaji A; Sureshkumar, Gopalsamy; Ly, Danith H

Anti-tumor Activity of miniPEG-γ-Modified PNAs to Inhibit MicroRNA-210 for Cancer Therapy

miniPEG-γ 修饰的 PNA 抑制 MicroRNA-210 的抗肿瘤活性,用于癌症治疗

Anisha Gupta, Elias Quijano, Yanfeng Liu, Raman Bahal, Susan E Scanlon, Eric Song, Wei-Che Hsieh, Demetrios E Braddock, Danith H Ly, W Mark Saltzman, Peter M Glazer